Enzyme replacement therapy 
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 4 Companies   3 Products   3 Products   22 Diseases   9 Trials   88 News 

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Creon (pancrelipase delayed-release) / AbbVie, Eisai           
          
            
             
Fabrazyme (agalsidase beta) / Sanofi           
          
            
             
Replagal (agalsidase alfa) / Samaritan Pharma, Takeda           
          
            
             
Aldurazyme (laronidase) / BioMarin, Sanofi           
          
            
             
Strensiq (asfotase alfa) / AstraZeneca           
          
            
             
Cerezyme (imiglucerase) / Sanofi           
          
            
             
Elelyso (taliglucerase alfa) / Pfizer           
          
            
             
Elfabrio (pegunigalsidase alfa-iwxj) / Protalix, Chiesi           
          
            
             
Sollpura (liprotamase) / Anthera Pharma           
          
            
             
Kanuma (sebelipase alfa) / AstraZeneca           
          
            
             
recombinant human arylsulfatase A (TAK-611) / Takeda           
          
            
             
INZ701 / Inozyme Pharma           
          
            
             
Izcargo (pabinafusp alfa) / JCR Pharma           
          
            
             
Mepsevii (vestronidase alfa) / Ultragenyx, Amicus           
          
            
             
adrulipase alfa (FW-EPI) / First Wave Bio           
          
            
             
Naglazyme (galsulfase) / AnGes MG, BioMarin           
          
            
             
efzimfotase alfa (ALXN1850) / AstraZeneca           
          
            
             
recombinant human alkaline phosphatase intravenous (recAP) / AM Pharma           
          
            
             
CDX-6114 / Nestle           
          
            
             
Pertzye (pancrelipase) / Chiesi           
          
            
             
recombinant human heparan N-sulfatase (SHP610) / Takeda           
          
            
             
SB-913 / Sangamo Therap           
          
            
             
reveglucosidase alfa (BMN 701) / BioMarin           
          
            
             
tividenofusp alfa (DNL310) / Denali Therap           
          
            
             
Duoc-01 / Duke University Medical Center           
          
            
             
GLM101 / Glycomine           
          
            
             
JR-441 / JCR Pharma           
          
            
             
SOBI003 / SOBI           
          
            
             
UX053 / Ultragenyx, Arcturus Therap           
          
            
             
intestinal alkaline phosphatase delayed release (SYN-020) / Theriva Bio           
          
            
             
pegtarviliase (AGLE-177) / Aeglea           
          
            
             
recombinant-iduronate-2-sulfatase (JR-032) / GSK, JCR Pharma           
          
            
             
ANG003 / Anagram Therap           
          
            
             
CAN103 / CANbridge Pharma           
          
            
             
Fabagal (fabrazyme biosimilar) / ISU Abxis           
          
            
             
N-sulphoglucosamine sulphohydrolase (DNL126) / Denali Therap           
          
            
             
recombinant lipase (CDX-7108) / Codexis, Nestle