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Enzyme replacement therapy
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4 Companies
3 Products
3 Products
22 Diseases
9 Trials
88 News
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Creon
(pancrelipase delayed-release) / AbbVie, Eisai
Fabrazyme
(agalsidase beta) / Sanofi
Replagal
(agalsidase alfa) / Samaritan Pharma, Takeda
Aldurazyme
(laronidase) / BioMarin, Sanofi
Strensiq
(asfotase alfa) / AstraZeneca
Cerezyme
(imiglucerase) / Sanofi
Elelyso
(taliglucerase alfa) / Pfizer
Elfabrio
(pegunigalsidase alfa-iwxj) / Protalix, Chiesi
Sollpura
(liprotamase) / Anthera Pharma
Kanuma
(sebelipase alfa) / AstraZeneca
recombinant human arylsulfatase A
(TAK-611) / Takeda
INZ701
/ Inozyme Pharma
Izcargo
(pabinafusp alfa) / JCR Pharma
Mepsevii
(vestronidase alfa) / Ultragenyx, Amicus
adrulipase alfa
(FW-EPI) / First Wave Bio
Naglazyme
(galsulfase) / AnGes MG, BioMarin
efzimfotase alfa
(ALXN1850) / AstraZeneca
recombinant human alkaline phosphatase intravenous
(recAP) / AM Pharma
CDX-6114
/ Nestle
Pertzye
(pancrelipase) / Chiesi
recombinant human heparan N-sulfatase
(SHP610) / Takeda
SB-913
/ Sangamo Therap
reveglucosidase alfa
(BMN 701) / BioMarin
tividenofusp alfa
(DNL310) / Denali Therap
Duoc-01
/ Duke University Medical Center
GLM101
/ Glycomine
JR-441
/ JCR Pharma
SOBI003
/ SOBI
UX053
/ Ultragenyx, Arcturus Therap
intestinal alkaline phosphatase delayed release
(SYN-020) / Theriva Bio
pegtarviliase
(AGLE-177) / Aeglea
recombinant-iduronate-2-sulfatase
(JR-032) / GSK, JCR Pharma
ANG003
/ Anagram Therap
CAN103
/ CANbridge Pharma
Fabagal
(fabrazyme biosimilar) / ISU Abxis
N-sulphoglucosamine sulphohydrolase
(DNL126) / Denali Therap
recombinant lipase
(CDX-7108) / Codexis, Nestle