Enzyme replacement therapy 
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Takeda           
          
            
Sanofi           
          
            
AstraZeneca           
          
            
BioMarin           
          
            
JCR Pharma           
          
            
Codexis           
          
            
Nestle           
          
            
Chiesi           
          
            
Denali Therap           
          
            
Ultragenyx           
          
            
AM Pharma           
          
            
AbbVie           
          
            
Amicus           
          
            
AnGes MG           
          
            
Anagram Therap           
          
            
Anthera Pharma           
          
            
Arcturus Therap           
          
            
CANbridge Pharma           
          
            
Duke University Medical Center           
          
            
Eisai           
          
            
Entero Therap           
          
            
GSK           
          
            
Glycomine           
          
            
ISU Abxis           
          
            
Inozyme Pharma           
          
            
Pfizer           
          
            
Protalix           
          
            
SOBI           
          
            
Samaritan Pharma           
          
            
Sangamo Therap           
          
            
Spyre Therap           
          
            
Theriva Bio