- |||||||||| Lipax (proliposomal intravesical paclitaxel) / TesoRx
Journal: AAV gene therapy for Tay-Sachs disease. (Pubmed Central) - Apr 27, 2022 Patient TSD-001 was treated at 30 months with an equimolar mix of AAVrh8-HEXA and AAVrh8-HEXB administered intrathecally (i.t.), with 75% of the total dose (1 × 10 vector genomes (vg)) in the cisterna magna and 25% at the thoracolumbar junction...TSD-002 developed anticonvulsant-responsive seizures at 2 years of age. This study provides early safety and proof-of-concept data in humans for treatment of patients with TSD by AAV gene therapy.
- |||||||||| Lipax (proliposomal intravesical paclitaxel) / TesoRx
Enrollment closed, Trial completion date, Trial primary completion date: Proliposomal Intravesical Paclitaxel for Treatment of Low-Grade, Stage Ta, Non Muscle Invasive Bladder Cancer (clinicaltrials.gov) - Sep 2, 2020 P1/2, N=15, Active, not recruiting, Persistence of paclitaxel in the voided urine at therapeutic concentrations up to 72 hours after instillation were observed. Recruiting --> Active, not recruiting | Trial completion date: May 2022 --> Aug 2022 | Trial primary completion date: May 2020 --> Aug 2020
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