- |||||||||| Amnolake (tamibarotene) / Syros
Abundance of Relapse-Predictive Cells Can be Estimated at Diagnosis and Is Strongly Associated with Outcome in Pediatric AML (Seaport Ballroom EFGH (Manchester Grand Hyatt San Diego)) - Nov 6, 2024 - Abstract #ASH2024ASH_1322; Patient-derived xenograft (PDX) models were treated with cytarabine (50 mg/kg/dose) or saline on days 1-4...The RARA/RXRA complex represses transcription in the absence of retinoic acid; transcription can be activated by the agonist tamibarotene (tami)...We validated the association of these cell types with chemoresistance in PDX models. We identified retinoic acid receptor agonism as a potential strategy to deplete one of these cell types.
- |||||||||| Translarna (ataluren) / PTC Therap, Amnolake (tamibarotene) / Syros
Journal: Photoinduced Cu(II)-Mediated Decarboxylative Thianthrenation of Aryl and Heteroaryl Carboxylic Acids. (Pubmed Central) - Jul 16, 2024 Mechanistic studies are in line with a reaction occurring through a photoinduced ligand-to-metal charge transfer (LMCT) of Cu(II)-arylcarboxylates, enabling radical decarboxylative carbometallation to form arylcopper(II) intermediates that in turn react with thianthrene to form the product. Noteworthy, the susceptibility of aryl thianthrenium salts to photodegradation is overcome by a Cu(I)-driven salvage loop, which continuously intercepts the transiently formed radicals and regenerates the products.
- |||||||||| Amnolake (tamibarotene) / Syros
Biomarker, Journal: Identification of shared disease marker genes and underlying mechanisms between rheumatoid arthritis and Crohn disease through bioinformatics analysis. (Pubmed Central) - Jun 28, 2024 Finally, tamibarotene, retinoic acid, and benzo[a]pyrene were identified as potential treatment options for patients with both RA and CD...Interestingly, the study has highlighted hsa-miR-31-5p as a potential key player in the common mechanism of both diseases, representing a new direction in research and a potential therapeutic target. These shared genes, potential mechanisms, and regulatory networks offer new opportunities for further research and may provide hope for future treatment of patients with both RA and CD.
- |||||||||| Amnolake (tamibarotene) / Syros
Review, Journal: How Do Retinoids Affect Alzheimer's Disease and Can They Be Novel Drug Candidates? (Pubmed Central) - Apr 4, 2024 This means that when administering these agents, their actions are to target a single disease-causing pathway at a time but do not affect other pathways. On the other hand, tamibarotene is a novel drug candidate that targets a range of pathways at once and provides a more comprehensive approach in its pharmacological actions.
- |||||||||| Amnolake (tamibarotene) / Syros
Trial completion date, Trial primary completion date, Combination therapy: SELECT-AML-1: Tamibarotene Plus Venetoclax/Azacitidine in Participants with Newly Diagnosed AML (clinicaltrials.gov) - Feb 22, 2024 P2, N=95, Recruiting, This is considered a valuable case for accumulating information on the treatment of CD56-positive APL resistant to ATRA and ATO. Trial completion date: Apr 2024 --> Apr 2028 | Trial primary completion date: Apr 2024 --> Apr 2028
- |||||||||| Amnolake (tamibarotene) / Syros
Journal: Blood transcriptome analysis uncovered COVID-19-myocarditis crosstalk. (Pubmed Central) - Feb 20, 2024 TBKBP1 and ERGIC1 were identified as crucial genes in the development of COVID-19-related myocarditis and have demonstrated a strong association with innate antiviral immunity. The present work may be helpful for further investigation of the molecular mechanisms and new therapeutic drug targets correlated with myocarditis in COVID-19.
- |||||||||| Targretin oral (bexarotene oral) / ReXceptor, Amnolake (tamibarotene) / Syros
Review, Journal: Retinoid Therapy for Neuroblastoma: Historical Overview, Regulatory Challenges, and Prospects. (Pubmed Central) - Feb 10, 2024 To promote isotretinoin use in Japan as a treatment for neuroblastoma, our clinical research team is planning to launch an investigator-initiated, registration-directed clinical trial. The present review article discusses the basic science behind retinoid therapy, pre-clinical/clinical evidence on neuroblastoma, the concept of the proposed clinical trial, and prospects for this therapy.
- |||||||||| Nypta (tideglusib) / ASD Therap, Amnolake (tamibarotene) / Syros
Journal: Cocktail Cell-Reprogrammed Hydrogel Microspheres Achieving Scarless Hair Follicle Regeneration. (Pubmed Central) - Jan 16, 2024 In vitro and in vivo studies show that AHFS can regulate fibroblast fate, induce fibroblast-to-DPC reprogramming by activating the PI3K/AKT pathway, finally promoting wound healing and in situ HF regeneration while inhibiting scar formation in a two-pronged translational approach. In conclusion, AHFS provides a new and effective strategy for functional repair of skin wounds.
- |||||||||| Amnolake (tamibarotene) / Syros, Nippon Shinyaku, Zeria Pharma, RaQualia, Ohara Pharma
Journal, Combination therapy: Use of tamibarotene, a potent and selective RAR? agonist, in combination with azacitidine in patients with relapsed and refractory AML with RARA gene overexpression. (Pubmed Central) - Dec 18, 2023 P2 In conclusion, AHFS provides a new and effective strategy for functional repair of skin wounds. In 21 response-evaluable patients, the complete remission/complete remission with incomplete hematologic recovery (CR/CRi) rate was 19%, and median time to initial CR/CRi was 1.2
- |||||||||| Venclexta (venetoclax) / Roche, AbbVie, Amnolake (tamibarotene) / Syros
Enrollment change, Trial completion date, Trial initiation date, Trial withdrawal, Trial primary completion date, Combination therapy: Phase I/II Study of SY-1425 (Tamibarotene) in Combination With Azacitidine and Venetoclax for Patients With Chronic Myelomonocytic Leukemia (clinicaltrials.gov) - Oct 25, 2023 P1/2, N=0, Withdrawn, In 21 response-evaluable patients, the complete remission/complete remission with incomplete hematologic recovery (CR/CRi) rate was 19%, and median time to initial CR/CRi was 1.2 Not yet recruiting --> Withdrawn | N=52 --> 0 | Trial completion date: Jan 2030 --> Oct 2023 | Initiation date: Mar 2024 --> Sep 2023 | Trial primary completion date: Jan 2028 --> Oct 2023
- |||||||||| peretinoin (K-333) / Kowa, Bay11-7082 / Bayer, Amnolake (tamibarotene) / Syros, Nippon Shinyaku, Zeria Pharma, RaQualia, Ohara Pharma
Preclinical, Journal: Acyclic retinoid peretinoin reduces hemorrhage-associated brain injury in vitro and in vivo. (Pubmed Central) - Oct 22, 2023 Not yet recruiting --> Withdrawn | N=52 --> 0 | Trial completion date: Jan 2030 --> Oct 2023 | Initiation date: Mar 2024 --> Sep 2023 | Trial primary completion date: Jan 2028 --> Oct 2023 On the other hand, nuclear factor-?B (NF-?B) inhibitors such as pyrrolidine dithiocarbamate (50
- |||||||||| An Update on Higher Risk Myelodysplastic Syndromes () - Aug 31, 2023 - Abstract #SOHO2023SOHO_939;
Therapies The current treatment landscape for HR-MDS is limited to HMA monotherapy, either parenteral (azacitidine or decitabine) or a more recently available oral option (decitabine/cedazuridine), followed by allogeneic hematopoietic stem cell transplant when feasible based on patient fitness and donor availability.14,15 There is a great need for alternative agents in the front-line and HMA-failure settings, as outcomes are particularly dismal in the latter.16,17 Unfortunately, drug development in MDS has been hampered by poorly-understood disease biology, lack of quality animal models, broad heterogeneity in disease phenotype, and suboptimal patient accrual to trials.18,19 Therapies more recently approved in AML are now being evaluated in HR-MDS. Liposomal daunorubicin/cytarabine (CPX-351) in the front-line setting has some promising, albeit limited, data published so far.20
- |||||||||| Vesanoid (tretinoin) / Roche, Amnolake (tamibarotene) / Syros, Nippon Shinyaku, Zeria Pharma, RaQualia, Ohara Pharma
Review, Journal: The Promise of Retinoids in the Treatment of Cancer: Neither Burnt Out Nor Fading Away. (Pubmed Central) - Jul 29, 2023 through strong SE levels in the gene locus and increased sensitivity to tamibarotene. Combined with a hypomethylating agent, synthetic retinoids have shown synergistic anti-leukemic effects in non-APL AML preclinical models and are now being studied in phase II and III clinical trials.
- |||||||||| Amnolake (tamibarotene) / Syros, Nippon Shinyaku, Zeria Pharma, RaQualia, Ohara Pharma
Journal: Tamibarotene targets heparin-binding protein for attenuating lung injury in sepsis. (Pubmed Central) - Jul 13, 2023 Combined with a hypomethylating agent, synthetic retinoids have shown synergistic anti-leukemic effects in non-APL AML preclinical models and are now being studied in phase II and III clinical trials. These findings demonstrated that tamibarotene lessens sepsis-induced lung injury, and the effect could be exerted by targeting HBP and thereby deregulating the NF-?B signaling pathway.
- |||||||||| Amnolake (tamibarotene) / Syros, Nippon Shinyaku, Zeria Pharma, RaQualia, Ohara Pharma
Journal: Integrated Analysis of Bulk RNA-Seq and Single-Cell RNA-Seq Unravels the Influences of SARS-CoV-2 Infections to Cancer Patients. (Pubmed Central) - Dec 24, 2022 The candidate drug molecules (e.g., Tamibarotene CTD 00002527) obtained by this study might be helpful for effective therapeutic targets in COVID-19 patients with cancer...Specifically, changes in the expression level of TNFSF10 in monocytes can be considered as an immune signature in COVID-19 patients with hematologic cancer. Targeting N-methyladenosine (m6A) pathways (e.g., METTL3/SERPINA1 axis) to restrict SARS-CoV-2 reproduction has therapeutic potential for COVID-19 patients.
- |||||||||| Amnolake (tamibarotene) / Syros, Nippon Shinyaku, Zeria Pharma, RaQualia
Journal: Identification of significant modules and hub genes involved in hepatic encephalopathy using WGCNA. (Pubmed Central) - Nov 25, 2022 Our study not only promoted the current understanding of neuroinflammation in HE, but also provided the first evidence that CYBB and FOXO1 played pivotal roles in the pathogenesis of HE, which might be potential biomarkers and therapeutic targets. Tamibarotene might be a novel drug compound against HE.
- |||||||||| Venclexta (venetoclax) / Roche, AbbVie, Amnolake (tamibarotene) / TMRC, Syros, Nippon Shinyaku, Zeria Pharma
Clinical, P2 data, Clinical Trial,Phase II, Journal, Combination therapy: AML-108 SELECT-AML-1 Trial in Progress: A Phase 2 Study of Tamibarotene in Combination With Venetoclax and Azacitidine in Previously Untreated Adult Patients Selected for RARA-Positive AML who are Ineligible for Standard Induction Therapy. (Pubmed Central) - Sep 29, 2022 P2 U.S. and France.
- |||||||||| Amnolake (tamibarotene) / TMRC, Syros, Nippon Shinyaku, Zeria Pharma
Clinical, P3 data, Clinical Trial,Phase III, Journal: MDS-110 SELECT-MDS-1 Trial in Progress: A Phase 3 Randomized, Double-Blind, Placebo-Controlled Study of Tamibarotene/Azacitidine Versus Placebo/Azacitidine in Newly Diagnosed Adult Patients Selected for RARA-Positive Higher-Risk MDS. (Pubmed Central) - Sep 29, 2022 P3 Azacitidine will be administered at 75 mg/m IV/SC daily on days 1-7 (or 1-5, 8-9) followed by tamibarotene/placebo at 6 mg BID orally on days 8-28 of each 28-day cycle. Response is assessed per the modified IWG MDS criteria (Cheson 2006).
- |||||||||| Amnolake (tamibarotene) / TMRC, Syros, Nippon Shinyaku, Zeria Pharma
A RANDOMIZED, DOUBLE-BLIND, PHASE 3 STUDY OF TAMIBAROTENE/AZACITIDINE VERSUS PLACEBO/AZACITIDINE IN NEWLY DIAGNOSED ADULT PATIENTS SELECTED FOR RARA-POSITIVE HR-MDS (SELECT-MDS-1) () - May 13, 2022 - Abstract #EHA2022EHA_1786; P3 Results Approximately 190 patients will be randomized 2:1 and stratified by IPSS-R risk group and geographic region, providing 90% power to detect the difference in CR rates between the experimental and control arms, respectively, with one-sided alpha of 0.025. Conclusion The SELECT-MDS-1 trial opened to enrollment in February 2021, recruitment is ongoing, with sites located in North America, Israel, and Europe (NCT04797780).
- |||||||||| Amnolake (tamibarotene) / TMRC, Syros, Nippon Shinyaku, Zeria Pharma
A randomized, double-blind, placebo-controlled study of tamibarotene/azacitidine versus placebo/azacitidine in newly diagnosed adult patients selected for RARA+ HR-MDS (SELECT-MDS-1). (Available On Demand; 300a) - Apr 28, 2022 - Abstract #ASCO2022ASCO_4312; P3 Response will be assessed per modified IWG MDS criteria (Cheson 2006). The SELECT-MDS-1 trial opened in February 2021, recruitment is ongoing, with sites located in North America, Israel, and Europe.
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