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15 Diseases
6 Trials
6 Trials
177 News
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Active industry trials
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Central Nervous System Diseases
Genetic Diseases, Inborn
Brain Diseases
Metabolic Diseases
Amino Acid Metabolism, Inborn Errors
Brain Diseases, Metabolic
Brain Diseases, Metabolic, Inborn
Inborn Amino Acid Metabolism Disorder
Metabolism, Inborn Errors
Urea Cycle Disorders
Urea Cycle Disorders, Inborn
Digestive System Diseases
Gastrointestinal Diseases
Hyperammonemia
Liver Diseases