Metabolism, Inborn Errors
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Generic mfg.           
          
            
Sanofi           
          
            
Merck (MSD)           
          
            
BioMarin           
          
            
AstraZeneca           
          
            
Chiesi           
          
            
GSK           
          
            
Pfizer           
          
            
Amgen           
          
            
Horizon Therapeutics           
          
            
Novartis           
          
            
Roche           
          
            
Amicus           
          
            
Astellas           
          
            
Takeda           
          
            
Ultragenyx           
          
            
Dr. Reddy’s           
          
            
GC Biopharma           
          
            
J&J           
          
            
JCR Pharma           
          
            
Kissei           
          
            
Kyowa Kirin           
          
            
Protalix           
          
            
Regeneron           
          
            
SOBI           
          
            
Sumitomo Pharma           
          
            
Zydus Lifesci           
          
            
AbbVie           
          
            
Abionyx Pharma           
          
            
Affibody           
          
            
Alcyone           
          
            
Amryt           
          
            
AnGes MG           
          
            
Anji Pharma           
          
            
Annovis Bio           
          
            
Astria Therap           
          
            
Bayer           
          
            
BioCryst           
          
            
Biogen           
          
            
Bora Pharma           
          
            
BridgeBio           
          
            
CANbridge Pharma           
          
            
Capstone           
          
            
Corino Therap           
          
            
CymaBay           
          
            
Daiichi Sankyo           
          
            
DalCor           
          
            
Eisai           
          
            
Enteris           
          
            
Huadong Medicine           
          
            


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