Inborn Amino Acid Metabolism Disorder  >>  sodium phenylbutyrate  >>  Phase 3
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2 Trials

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Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
sodium phenylbutyrate / Generic mfg.
NCT00992459: Efficacy and Safety of HPN-100 for the Treatment of Adults With Urea Cycle Disorders

Completed
3
46
US, Canada
HPN-100, GT4P, glyceryl tri-(4-phenylbutyrate), Buphenyl (NaPBA), sodium phenylbutyrate
Horizon Pharma Ireland, Ltd., Dublin Ireland
Urea Cycle Disorders
09/10
09/10
NCT01529060: Phenylbutyrate Therapy for Maple Syrup Urine Disease

Completed
2/3
20
US
Phenylbutyrate, Buphenyl-TM, Placebo powder
Brendan Lee
Maple Syrup Urine Disease
09/17
12/17

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