Zentrum für Kinder- und Jugendmedizin Angelika-Lautenschläger-Klinik
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 0 Trials 
4 Trials

   

Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
Opladen, Thomas
NCT05099640 / 2021-000474-29: A Study of PTC923 in Participants With Phenylketonuria

Completed
3
157
Europe, Canada, US, RoW
PTC923, Placebo
PTC Therapeutics
Phenylketonuria
04/23
05/23
NCT05166161 / 2021-000497-28: A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria

Recruiting
3
200
Europe, Canada, Japan, US, RoW
PTC923, Sepiapterin
PTC Therapeutics
Phenylketonuria
04/26
04/26
NCT03758521: Natural History Study of Patients with Succinic Semialdehyde Dehydrogenase (SSADH) Deficiency

Active, not recruiting
N/A
55
Europe, US
Transcranial magnetic stimulation (TMS), Nexstim Navigated Brain Stimulation (NBS) System 4, Magnetic resonance imaging (MRI), Electroencephalogram (EEG), Natus, Bio-specimen Collection
Boston Children's Hospital, Washington State University, University of South Florida, University Hospital Heidelberg, Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
Succinic Semialdehyde Dehydrogenase Deficiency
05/29
06/29
Jeltsch, Kathrin
NCT03758521: Natural History Study of Patients with Succinic Semialdehyde Dehydrogenase (SSADH) Deficiency

Active, not recruiting
N/A
55
Europe, US
Transcranial magnetic stimulation (TMS), Nexstim Navigated Brain Stimulation (NBS) System 4, Magnetic resonance imaging (MRI), Electroencephalogram (EEG), Natus, Bio-specimen Collection
Boston Children's Hospital, Washington State University, University of South Florida, University Hospital Heidelberg, Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
Succinic Semialdehyde Dehydrogenase Deficiency
05/29
06/29

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