Mucopolysaccharidosis Type IIIB
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 3 Companies   2 Products   2 Products   0 Mechanisms of Action   0 Trials   22 News 
  • ||||||||||  NN1213 / Novo Nordisk
    Trial completion date, Trial termination, Trial primary completion date:  Natural History Study to Characterise the Course of Disease Progression in Participants With Mucopolysaccharidosis Type IIIB (clinicaltrials.gov) -  Sep 13, 2018   
    P=N/A,  N=30, Terminated, 
    Trial completion date: Apr 2018 --> Jul 2017 | Active, not recruiting --> Terminated | Trial primary completion date: Apr 2018 --> Jul 2017; The Sponsor's decision to terminate the SBC-103 program was reached after review of the data from all interventional clinical studies of SBC-103.
  • ||||||||||  lesinidase alfa (SBC-103) / AstraZeneca
    Trial completion, Trial primary completion date:  Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 in Mucopolysaccharidosis III, Type B (MPS IIIB) (clinicaltrials.gov) -  Jul 12, 2018   
    P1/2,  N=11, Completed, 
    Trial completion date: Apr 2018 --> Jul 2017 | Active, not recruiting --> Terminated | Trial primary completion date: Apr 2018 --> Jul 2017; The Sponsor's decision to terminate the SBC-103 program was reached after review of the data from all interventional clinical studies of SBC-103. Active, not recruiting --> Completed | Trial primary completion date: Jul 2018 --> Oct 2017
  • ||||||||||  SAF-301 / Lysogene, Alcyone
    Enrollment closed, Trial primary completion date, Gene therapy:  Long-term Follow-up of Sanfilippo Type A Patients Treated by Intracerebral SAF-301 Gene Therapy (clinicaltrials.gov) -  Jan 18, 2017   
    P1/2,  N=4, Active, not recruiting, 
    Active, not recruiting --> Completed | Trial primary completion date: Jul 2018 --> Oct 2017 Completed --> Active, not recruiting | Trial primary completion date: May 2016 --> May 2017
  • ||||||||||  Trial completion:  Natural History Studies of Mucopolysaccharidosis III (clinicaltrials.gov) -  Nov 16, 2015   
    P=N/A,  N=25, Completed, 
    Initiation date: Oct 2013 --> May 2013 | Trial primary completion date: Jun 2017 --> May 2016 Recruiting --> Completed
  • ||||||||||  Trial initiation date, Trial primary completion date:  Natural History Studies of Mucopolysaccharidosis III (clinicaltrials.gov) -  Feb 12, 2015   
    P=N/A,  N=30, Recruiting, 
    Trial primary completion date: Jun 2014 --> Jun 2017 Initiation date: Aug 2013 --> Feb 2014 | Trial primary completion date: Jul 2015 --> Oct 2015
  • ||||||||||  Enrollment open:  Natural History Studies of Mucopolysaccharidosis III (clinicaltrials.gov) -  Jan 14, 2014   
    P=N/A,  N=30, Recruiting, 
    Recruiting --> Active, not recruiting Not yet recruiting --> Recruiting
  • ||||||||||  SAF-301 / Lysogene, Alcyone
    Trial completion, Gene therapy, Viral vector:  Intracerebral Gene Therapy for Sanfilippo Type A Syndrome (clinicaltrials.gov) -  Jul 8, 2013   
    P1/2,  N=4, Completed, 
    Not yet recruiting --> Recruiting Active, not recruiting --> Completed