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20 Products
157 Diseases
20 Products
113 Trials
5094 News
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Phase
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Trials
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24
36
48
60
72
84
96
108
120
Talzenna
(talazoparib) / Pfizer
Kuvan
(sapropterin) / BioMarin, Daiichi Sankyo
Aldurazyme
(laronidase) / BioMarin, Sanofi
Palynziq
(pegvaliase-pqpz) / BioMarin
Firdapse
(amifampridine) / BioMarin, Catalyst Pharma, Dydo Pharma
Vimizim
(elosulfase alfa) / BioMarin
Voxzogo
(vosoritide) / BioMarin
Kyndrisa
(drisapersen) / BioMarin
Roctavian
(valoctocogene roxaparvovec-rvox) / BioMarin
Brineura
(cerliponase alfa) / BioMarin
Naglazyme
(galsulfase) / AnGes MG, BioMarin
tralesinidase alfa
(AX 250) / Allievex Corp
BMN 044
/ BioMarin
reveglucosidase alfa
(BMN 701) / BioMarin
BMN 331
/ BioMarin
domofenogene zalfaparvovec
(BMN 307) / BioMarin
BMN 045
/ BioMarin
BMN 053
/ BioMarin
BMN 255
/ BioMarin
BMN 351
/ BioMarin