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 20 Products   157 Diseases   20 Products   113 Trials   5094 News 

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 Phase 
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 Trials
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Talzenna (talazoparib) / Pfizer           
          
            
             
Kuvan (sapropterin) / BioMarin, Daiichi Sankyo           
          
            
             
Aldurazyme (laronidase) / BioMarin, Sanofi           
          
            
             
Palynziq (pegvaliase-pqpz) / BioMarin           
          
            
             
Firdapse (amifampridine) / BioMarin, Catalyst Pharma, Dydo Pharma           
          
            
             
Vimizim (elosulfase alfa) / BioMarin           
          
            
             
Voxzogo (vosoritide) / BioMarin           
          
            
             
Kyndrisa (drisapersen) / BioMarin           
          
            
             
Roctavian (valoctocogene roxaparvovec-rvox) / BioMarin           
          
            
             
Brineura (cerliponase alfa) / BioMarin           
          
            
             
Naglazyme (galsulfase) / AnGes MG, BioMarin           
          
            
             
tralesinidase alfa (AX 250) / Allievex Corp           
          
            
             
BMN 044 / BioMarin           
          
            
             
reveglucosidase alfa (BMN 701) / BioMarin           
          
            
             
BMN 331 / BioMarin           
          
            
             
domofenogene zalfaparvovec (BMN 307) / BioMarin           
          
            
             
BMN 045 / BioMarin           
          
            
             
BMN 053 / BioMarin           
          
            
             
BMN 255 / BioMarin           
          
            
             
BMN 351 / BioMarin