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Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
LB-001 / AstraZeneca
SUNRISE, NCT04581785: Gene Therapy With hLB-001 in Pediatric Patients With Severe Methylmalonic Acidemia	Terminated	1/2	4	US	hLB-001	LogicBio Therapeutics, Inc, Alexion Pharmaceuticals, Inc.	Methylmalonic Acidemia	01/23	01/23
NCT05506254: Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy	Active, not recruiting	N/A	4	US	hLB-001	LogicBio Therapeutics, Inc, Alexion Pharmaceuticals, Inc.	Methylmalonic Acidemia	12/37	12/37