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Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
Upstaza (eladocagene exuparvovec) / PTC Therap
NCT02926066 / 2019-003072-39: A Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC - An Expansion	Completed	2	12	RoW	AAV2-hAADC	National Taiwan University Hospital, PTC Therapeutics	Aromatic Amino Acid Decarboxylase Deficiency	01/22	05/22
NCT04903288: A Study of SmartFlow Magnetic Resonance (MR) Compatible Ventricular Cannula for Administering Eladocagene Exuparvovec to Pediatric Participants	Active, not recruiting	2	13	US, RoW	Eladocagene Exuparvovec	PTC Therapeutics	AADC Deficiency	05/23	04/28
NCT01395641 / 2019-003032-23: A Phase I/II Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC	Completed	1/2	10	RoW	gene therapy, Intracerebral infusion of AAV2-hAADC viral vector	National Taiwan University Hospital, PTC Therapeutics	Aromatic L-amino Acid Decarboxylase (AADC) Deficiency	12/20	03/22
NCT02852213: A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients	Recruiting	1	42	US	AAV2-hAADC, Adeno Virus Human Aromatic L-Amino Acid Decarboxylase	Krzysztof Bankiewicz, National Institute of Neurological Disorders and Stroke (NINDS), University of California, San Francisco	AADC Deficiency	07/27	07/31