Amvuttra (vutrisiran) / Alnylam 
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4 Trials

   

Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
Amvuttra (vutrisiran) / Alnylam
HELIOS-A, NCT03759379 / 2018-002098-23: A Study of Vutrisiran (ALN-TTRSC02) in Patients With Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis)

Active, not recruiting
3
164
Europe, Canada, Japan, US, RoW
Patisiran, ONPATTRO, ALN-TTR02, Vutrisiran, ALN-TTRSC02, AMVUTTRA
Alnylam Pharmaceuticals
Amyloidosis, Hereditary, Transthyretin Amyloidosis
11/20
10/26
HELIOS-B, NCT04153149 / 2019-003153-28: A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy

Active, not recruiting
3
655
Europe, Canada, Japan, US, RoW
Vutrisiran, ALN-TTRSC02, Sterile Normal Saline (0.9% NaCl)
Alnylam Pharmaceuticals
Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
05/24
12/26
NCT06679946: A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy

Enrolling by invitation
3
800
Europe, US, RoW
Vutrisiran, ALN-TTRSC02, AMVUTTRA®
Alnylam Pharmaceuticals
Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
06/28
06/28
MyocardON-TTR, NCT05873868: Myocardial Effects in Patients with ATTRv with Polyneuropathy Treated with Patisiran or Vutrisiran

Recruiting
N/A
20
Europe
Six minutes walk test, Kansas City questionnaire, COMPASS31 self questionnaire
Rennes University Hospital
Transthyretin Amyloidosis, Amyloidosis, Hereditary
02/26
07/26

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