Exondys 51 (eteplirsen) / Sarepta Therap 
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 9 Diseases   3 Trials   3 Trials   284 News 

Disease Category View   Disease View
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 Phase 
N/A
1
2
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4
 Trials
 02468101214161820
            
                                                                                                      
            
Duchenne Muscular Dystrophy           
          
            
            
Atrophy           
          
            
            
Becker Muscular Dystrophy           
          
            
            
Genetic Diseases, Inborn           
          
            
            
Genetic Diseases, X-Linked           
          
            
            
Muscular Diseases           
          
            
            
Muscular Disorders, Atrophic           
          
            
            
Muscular Dystrophies           
          
            
            
Muscular Dystrophy, Duchenne