AAVrh.10CUCLN2 / REGENXBIO 
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  • ||||||||||  AAVrh.10CUCLN2 / REGENXBIO
    Enrollment closed, Trial initiation date:  AAVRh.10 Administered to Children With Late Infantile Neuronal Ceroid Lipofuscinosis (clinicaltrials.gov) -  Jan 9, 2018   
    P1/2,  N=8, Active, not recruiting, 
    Active, not recruiting --> Completed Recruiting --> Active, not recruiting | Initiation date: Dec 2010 --> Apr 2010