Dojolvi (triheptanoin) / Ultragenyx 
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 30 Diseases   10 Trials   10 Trials   301 News 

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Epilepsy           
          
            
            
Genetic Diseases, Inborn           
          
            
            
Carbohydrate Metabolism, Inborn Errors           
          
            
            
Glucose Transporter Type 1 Deficiency Syndrome           
          
            
            
Metabolism, Inborn Errors           
          
            
            
Metabolic Diseases           
          
            
            
Syndrome           
          
            
            
Basal Ganglia Diseases           
          
            
            
Brain Diseases           
          
            
            
Cardiomyopathies           
          
            
            
Central Nervous System Diseases           
          
            
            
Chorea           
          
            
            
Cognition Disorders           
          
            
            
Delirium, Dementia, Amnestic, Cognitive Disorders           
          
            
            
Dementia           
          
            
            
Dyskinesias           
          
            
            
Ganglion Cysts           
          
            
            
Glycogen Storage Disease           
          
            
            
Glycogen Storage Disease Type 4           
          
            
            
Glycogen Storage Disease Type IV           
          
            
            
Heart Diseases           
          
            
            
Heart Failure           
          
            
            
Heredodegenerative Disorders, Nervous System           
          
            
            
Huntington Disease           
          
            
            
LCHAD Deficiency           
          
            
            
Movement Disorders           
          
            
            
Neurodegenerative Diseases           
          
            
            
Polyglucosan Body Disease, Adult           
          
            
            
Synovial Cyst           
          
            
            
VLCAD Deficiency