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73 Diseases
12 Trials
12 Trials
976 News
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Active industry trials
Active owner-sponsored trials
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Genetic Diseases, Inborn
Iron Overload
Metabolic Diseases
Thalassemia
Iron Metabolism Disorders
Hematologic Diseases
Hemoglobinopathies
Anemia, Hemolytic
Anemia, Hemolytic, Congenital
Hemolysis
Beta-Thalassemia
Anemia
Central Nervous System Diseases
Movement Disorders
Neurodegenerative Diseases
Brain Diseases
Spinal Cord Diseases
Acquired Immunodeficiency Syndrome
Acute Kidney Injury
Ataxia
Cerebellar Ataxia
Cerebellar Diseases
Communicable Diseases
Dyskinesias
Friedreich ataxia
Hemochromatosis
Heredodegenerative Disorders, Nervous System
Human Immunodeficiency Virus
Immunologic Deficiency Syndromes
Kidney Diseases
Metabolism, Inborn Errors
Metal Metabolism, Inborn Errors
Mitochondrial Diseases
Neutropenia
Renal Insufficiency
Spinocerebellar Ataxias
Spinocerebellar Degenerations
Urologic Diseases
Amyotrophic Lateral Sclerosis
Anemia, Sickle Cell
Basal Ganglia Diseases
Bone Diseases
Bone Diseases, Metabolic
Bone Marrow Diseases
Digestive System Diseases
Ganglion Cysts
Gastrointestinal Diseases
Heart Diseases
Hemosiderosis
Hepatic Insufficiency
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