- |||||||||| fresolimumab (GC 1008) / Sanofi
Pharmacological suppression of cancer associated fibroblast (CAF)-driven tumor fibrosis identified by the PRO-C3 biomarker in NSCLC (Foyer) - Feb 5, 2026 - Abstract #ELCC2026ELCC_842; CAFs were treated with the ALK5/TGF-?1 receptor kinase inhibitor (ALK5i) or Fresolimumab (antibody targetingTGF-?) to investigate if the PRO-C3 and collagen deposition could be pharmacologically modified by therapeutic intervention.Results PRO-C3 was produced by lung CAFs after activation with TGF-beta but not PDGF-AB, IL-1 and IL-6 (p<0.0001)...These findings support that modulating CAFs can be monitored in vitro and that treating tumor fibrosis in NSCLC may be achived. Here, PRO-C3 may support drug development efforts already from drug discovery through clinical evaluation.
- |||||||||| fresolimumab (GC 1008) / Sanofi
Journal: In-silico prediction of TGF-?1 non-synonymous variants and their impact on binding affinity to Fresolimumab. (Pubmed Central) - Nov 21, 2024 Among them, the E35D variant significantly destabilized the TGF-?1 protein structure, resulting in rearrangement in the binding site and affecting the interactions with the Fresolimumab. This study identified four variants that can affect the TGF-?1 protein structure and result in functional consequences such as impaired response to Fresolimumab.Communicated by Ramaswamy H. Sarma.
- |||||||||| fresolimumab (GC 1008) / Sanofi
Trial completion, Trial completion date: Safety of Fresolimumab in the Treatment of Osteogenesis Imperfecta (clinicaltrials.gov) - Jul 6, 2022 P1, N=11, Completed, Such colocalized targeting elicits distinct and superior antitumor responses relative to single agent combination therapy. Active, not recruiting --> Completed | Trial completion date: Aug 2023 --> Jul 2022
- |||||||||| fresolimumab (GC 1008) / Sanofi
Variability of Proteinuria in Nephrotic Syndrome: GC1008 PH2 Trial in FSGS (Mini-Orals Hall) - May 5, 2022 - Abstract #ERAEDTA2022ERA_EDTA_1031; P2 These data suggest that labour intensive, cumbersome timed 24-h urine collections should not be performed in clinical trials of nephrotic syndrome patients. Importantly, these data should allow for more precise power and sample size estimates for future interventional clinical trials of nephrotic syndrome.
- |||||||||| fresolimumab (GC 1008) / Sanofi
Journal: Targeting transforming growth factor- β (TGF-β) for treatment of osteogenesis imperfecta. (Pubmed Central) - Apr 5, 2022 P1 Importantly, these data should allow for more precise power and sample size estimates for future interventional clinical trials of nephrotic syndrome. Our data confirm that TGF-β signaling is a driver pathogenic mechanism in OI bone and that anti-TGF-β therapy could be a potential disease-specific therapy with dose-dependent effects on bone mass and turnover.
- |||||||||| fresolimumab (GC 1008) / Sanofi
Enrollment closed, Enrollment change: Safety of Fresolimumab in the Treatment of Osteogenesis Imperfecta (clinicaltrials.gov) - Mar 28, 2022 P1, N=11, Active, not recruiting, Our data confirm that TGF-β signaling is a driver pathogenic mechanism in OI bone and that anti-TGF-β therapy could be a potential disease-specific therapy with dose-dependent effects on bone mass and turnover. Recruiting --> Active, not recruiting | N=16 --> 11
- |||||||||| Humira (adalimumab) / Eisai, AbbVie
Review, Journal: Interventions for focal segmental glomerulosclerosis in adults. (Pubmed Central) - Mar 8, 2022 The final study (109 participants) compared sparsentan, a dual inhibitor of endothelin Type A receptor and of the angiotensin II Type 1 receptor, with irbesartan...Treatment with cyclosporin for at least six months was more likely to achieve complete remission of proteinuria compared with other treatments but there was considerable imprecision due to few studies and small participant numbers. In future studies of existing or new interventions, the investigators must clearly define the populations included in the study to provide appropriate recommendations for patients with primary, genetic or secondary FSGS.
- |||||||||| bintrafusp alfa (M7824) / EMD Serono, Merck (MSD), vactosertib (TEW-7197) / National OncoVenture, Medpacto, fresolimumab (GC 1008) / Sanofi
Review, Journal: TGFβ-Directed Therapeutics: 2020. (Pubmed Central) - Nov 17, 2021 Two small molecule kinase inhibitors which block the serine-threonine kinase activity of TGFβRI on TGFβRII, a pan-TGFβ neutralizing antibody, a TGFβ trap, a TGFβ antisense agent, an antibody which stabilizes the latent complex of TGFβ and a fusion protein which neutralizes TGFβ and binds PD-L1 are in clinical development. The challenge is how to most effectively incorporate blocking TGFβ activity alone and in combination with other therapeutics to improve treatment outcome.
- |||||||||| disitertide (P144) / Avadel, Digna Biotech, fresolimumab (GC 1008) / Sanofi
Journal: Discovery of Selective Transforming Growth Factor β Type II Receptor Inhibitors as Antifibrosis Agents. (Pubmed Central) - Jun 1, 2021 In this report, we disclose selective TGF-β type II receptor (TGF-βRII) inhibitors that exhibited high functional selectivity in cell-based assays. The representative compound 29 attenuated collagen type I alpha 1 chain (COL1A1) expression in a mouse fibrosis model, which suggests that selective inhibition of TGF-βRII-dependent signaling could be a new treatment for fibrotic disorders.
- |||||||||| fresolimumab (GC 1008) / Sanofi
Trial completion date: Safety of Fresolimumab in the Treatment of Osteogenesis Imperfecta (clinicaltrials.gov) - Apr 22, 2021 P1, N=16, Recruiting, The representative compound 29 attenuated collagen type I alpha 1 chain (COL1A1) expression in a mouse fibrosis model, which suggests that selective inhibition of TGF-βRII-dependent signaling could be a new treatment for fibrotic disorders. Trial completion date: Oct 2022 --> Aug 2023
- |||||||||| fresolimumab (GC 1008) / Sanofi
Clinical, Journal, PD(L)-1 Biomarker, IO biomarker: Baseline T cell dysfunction by single cell network profiling in metastatic breast cancer patients. (Pubmed Central) - Jul 29, 2020 P2 Functional T cell analysis suggests that baseline T cell functionality is hampered in metastatic breast cancer patients, at least in part mediated by the PD-1 signaling pathway. These preliminary data support the rationale for investigating the possible beneficial effects of adding PD-1 blockade to improve responses to TGFβ blockade and radiotherapy.
- |||||||||| fresolimumab (GC 1008) / Sanofi
Trial completion date, Trial primary completion date: Safety of Fresolimumab in the Treatment of Osteogenesis Imperfecta (clinicaltrials.gov) - Apr 8, 2020 P1, N=16, Recruiting, Trial completion date: Jan 2020 --> Dec 2021 | Trial primary completion date: Jan 2020 --> Jun 2021 Trial completion date: Aug 2021 --> Oct 2022 | Trial primary completion date: Aug 2021 --> Aug 2022
- |||||||||| fresolimumab (GC 1008) / Sanofi
Trial completion date, Trial primary completion date: Safety of Fresolimumab in the Treatment of Osteogenesis Imperfecta (clinicaltrials.gov) - Jan 30, 2020 P1, N=16, Recruiting, Trial completion date: Aug 2021 --> Oct 2022 | Trial primary completion date: Aug 2021 --> Aug 2022 Trial completion date: Aug 2020 --> Aug 2021 | Trial primary completion date: Aug 2020 --> Aug 2021
- |||||||||| Orencia (abatacept) / BMS, Humira (adalimumab) / Eisai, AbbVie, Rituxan (rituximab) / Roche, Biogen
A SUCCESSFUL TREATMENT WITH ABATACEPT IN STEROID RESISTANT FOCAL SEGMENTAL GLOMERULOSCLEROSIS () - Oct 25, 2019 - Abstract #IPNA2019IPNA_20; Herein we present our experience with abatacept, a cytotoxic Tlymphocyte-associated antigen 4-immunoglobulin fusion protein (CTLA-4-Ig), in a patient diagnosed with primary FSGS and resistant to steroid, cyclosporine A (CsA), Mycofenolat mophetinile (MMF) and rituximab...After administration of abatacept, proteinuria level decreased below 1 gram/day and serum albumin levels increased to 3 mg/dL. This case indicates that abatacept can be at least partially effective in FSGS with resistance to other immunsupressive therapies such as CsA, cyclophosphamide, MMF and rituximab.
- |||||||||| fresolimumab (GC 1008) / Sanofi
Trial completion: Fresolimumab and Radiotherapy in Metastatic Breast Cancer (clinicaltrials.gov) - Mar 5, 2019 P2, N=23, Completed, This case indicates that abatacept can be at least partially effective in FSGS with resistance to other immunsupressive therapies such as CsA, cyclophosphamide, MMF and rituximab. Active, not recruiting --> Completed
- |||||||||| fresolimumab (GC 1008) / Sanofi
Trial completion date, Trial primary completion date: Safety of Fresolimumab in the Treatment of Osteogenesis Imperfecta (clinicaltrials.gov) - Jan 22, 2019 P1, N=16, Recruiting, Suspended --> Recruiting Trial completion date: Aug 2019 --> Aug 2020 | Trial primary completion date: Aug 2018 --> Aug 2020
- |||||||||| fresolimumab (GC 1008) / Sanofi
Trial initiation date: Safety of Fresolimumab in the Treatment of Osteogenesis Imperfecta (clinicaltrials.gov) - Sep 18, 2017 P1, N=16, Recruiting, However, fresolimumab was well tolerated and is appropriate for continued evaluation in larger studies with adequate power. Initiation date: Jul 2017 --> Nov 2017
- |||||||||| fresolimumab (GC 1008) / Sanofi
Phase classification, Trial primary completion date: Fresolimumab and Radiotherapy in Metastatic Breast Cancer (clinicaltrials.gov) - Oct 27, 2015 P2, N=24, Active, not recruiting, N=20 --> 14 Phase classification: P=N/A --> P2 | Trial primary completion date: Sep 2015 --> Jun 2014
- |||||||||| fresolimumab (GC 1008) / Sanofi
Trial termination: Anti-TGF-beta Therapy in Patients With Myelofibrosis (clinicaltrials.gov) - Dec 9, 2014 P1, N=3, Terminated, Active, not recruiting --> Completed Completed --> Terminated; Early termination when the drug was no longer made available by the pharmaceutical company due to unanticipated management and administrative decisions.
- |||||||||| fresolimumab (GC 1008) / Sanofi
Enrollment closed: Fresolimumab and Radiotherapy in Metastatic Breast Cancer (clinicaltrials.gov) - Sep 28, 2014 P=N/A, N=28, Active, not recruiting, Completed --> Terminated; Early termination when the drug was no longer made available by the pharmaceutical company due to unanticipated management and administrative decisions. Recruiting --> Active, not recruiting
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