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Brineura
(cerliponase alfa) /
BioMarin
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17 Diseases
2 Trials
2 Trials
209 News
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Active industry trials
Active owner-sponsored trials
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Trials
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1
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Adult Neuronal Ceroid Lipofuscinosis
Batten Disease
Ceroid Lipofuscinosis Neuronal 1
Ceroid Lipofuscinosis Neuronal 2
Ceroid Lipofuscinosis Neuronal 6
Ceroid Storage Disease
Genetic Diseases, Inborn
Heredodegenerative Disorders, Nervous System
Lipid Metabolism Disorders
Lipid Metabolism, Inborn Errors
Lipidoses
Metabolic Diseases
Metabolism, Inborn Errors
Neurodegenerative Diseases
Neuronal Ceroid-Lipofuscinoses
Sphingolipidoses
Spielmeyer-Vogt Disease