Brineura (cerliponase alfa) / BioMarin 
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 17 Diseases   2 Trials   2 Trials   209 News 

Disease Category View   Disease View
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 Phase 
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 Trials
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Adult Neuronal Ceroid Lipofuscinosis           
          
            
            
Batten Disease           
          
            
            
Ceroid Lipofuscinosis Neuronal 1           
          
            
            
Ceroid Lipofuscinosis Neuronal 2           
          
            
            
Ceroid Lipofuscinosis Neuronal 6           
          
            
            
Ceroid Storage Disease           
          
            
            
Genetic Diseases, Inborn           
          
            
            
Heredodegenerative Disorders, Nervous System           
          
            
            
Lipid Metabolism Disorders           
          
            
            
Lipid Metabolism, Inborn Errors           
          
            
            
Lipidoses           
          
            
            
Metabolic Diseases           
          
            
            
Metabolism, Inborn Errors           
          
            
            
Neurodegenerative Diseases           
          
            
            
Neuronal Ceroid-Lipofuscinoses           
          
            
            
Sphingolipidoses           
          
            
            
Spielmeyer-Vogt Disease