sapropterin / Generic mfg. 
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 56 Diseases   8 Trials   8 Trials   1230 News 

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 Trials
 036912151821242730
            
                                                                                                      
            
Metabolism, Inborn Errors           
          
            
            
Phenylketonurias           
          
            
            
Amino Acid Metabolism, Inborn Errors           
          
            
            
Brain Diseases           
          
            
            
Brain Diseases, Metabolic           
          
            
            
Brain Diseases, Metabolic, Inborn           
          
            
            
Central Nervous System Diseases           
          
            
            
Genetic Diseases, Inborn           
          
            
            
Inborn Amino Acid Metabolism Disorder           
          
            
            
Metabolic Diseases           
          
            
            
CNS Disorders           
          
            
            
Hypertension           
          
            
            
Autistic Disorder           
          
            
            
Child Development Disorders, Pervasive           
          
            
            
Developmental Disabilities           
          
            
            
Mental Disorders Diagnosed in Childhood           
          
            
            
Vascular Diseases           
          
            
            
Kidney Diseases           
          
            
            
Renal Insufficiency           
          
            
            
Renal Insufficiency, Chronic           
          
            
            
Urologic Diseases           
          
            
            
Albuminuria           
          
            
            
Atherosclerosis           
          
            
            
Autism Spectrum Disorder           
          
            
            
Chronic Disease           
          
            
            
Cystic Fibrosis           
          
            
            
Diabetes Mellitus           
          
            
            
Diabetes Mellitus, Type 2           
          
            
            
Digestive System Diseases           
          
            
            
Dihydropteridine Reductase Deficiency           
          
            
            
Dilatation, Pathologic           
          
            
            
Disease Attributes           
          
            
            
Fibrosis           
          
            
            
GTP Cyclohydrolase I Deficiency           
          
            
            
Gastrointestinal Diseases           
          
            
            
Heart Diseases           
          
            
            
Hypertension, Portal           
          
            
            
Hypertension, Pulmonary           
          
            
            
Idiopathic Pulmonary Hypertension           
          
            
            
Inflammation           
          
            
            
Kidney Failure, Chronic           
          
            
            
Liver Cirrhosis           
          
            
            
Liver Diseases           
          
            
            
Lung Diseases           
          
            
            
Lung Diseases, Obstructive           
          
            
            
Mental Retardation           
          
            
            
Proteinuria           
          
            
            
Psychotic Disorders           
          
            
            
Pulmonary Arterial Hypertension           
          
            
            
Pulmonary Disease, Chronic Obstructive           
          
            
            


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