2019-003529-36: A clinical study to evaluate the medicinal product in Patients with Propionic Acidemia |
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| Not yet recruiting | 1/2 | 36 | Europe | mRNA-3927, Injection | ModernaTX, Inc, ModernaTX, Inc. | Propionic Acidemia- Propionic acidemia is an autosomal recessive disorder caused by loss-of-function mutations in PCCA or PCCB (and in rare instances, mutations in both PCCA and PCCB), resulting in the loss of enzymatic activity of the mitochondrial complex PCC, Deficiency of PCCA and PCCB, Body processes [G] - Metabolic Phenomena [G03] | | | | |
