Liver Diseases  >>  rAAV1-CB-hAAT  >>  Phase 2
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2 Trials

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Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
rAAV1-CB-hAAT / BCM Families Foundation, AGTC
NCT01054339 / 2009-014286-20: Safety & Efficacy Study of rAAV1-CB-hAAT for Alpha-1 Antitrypsin Deficiency

Completed
2
9
US, Europe
rAAV1-CB-hAAT
Applied Genetic Technologies Corp, National Heart, Lung, and Blood Institute (NHLBI)
Alpha-1 Antitrypsin Deficiency
10/11
10/15
NCT00430768: Experimental Gene Transfer Procedure to Treat Alpha 1-Antitrypsin (AAT) Deficiency

Completed
1/2
9
US
rAAV1-CB-hAAT
University of Massachusetts, Worcester, National Heart, Lung, and Blood Institute (NHLBI), Applied Genetic Technologies Corp, Alpha-1 Foundation, University of Florida, National Center for Research Resources (NCRR)
Alpha 1-Antitrypsin Deficiency
01/15
01/15

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