| Completed | 2 | 9 | US, Europe | rAAV1-CB-hAAT | Applied Genetic Technologies Corp, National Heart, Lung, and Blood Institute (NHLBI) | Alpha-1 Antitrypsin Deficiency | 10/11 | 10/15 | | |
NCT00430768: Experimental Gene Transfer Procedure to Treat Alpha 1-Antitrypsin (AAT) Deficiency |
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| Completed | 1/2 | 9 | US | rAAV1-CB-hAAT | University of Massachusetts, Worcester, National Heart, Lung, and Blood Institute (NHLBI), Applied Genetic Technologies Corp, Alpha-1 Foundation, University of Florida, National Center for Research Resources (NCRR) | Alpha 1-Antitrypsin Deficiency | 01/15 | 01/15 | | |