| Completed | 3 | 77 | Europe, Canada, US, RoW | Viltolarsen, NS-065/NCNP-01, Placebo | NS Pharma, Inc., Nippon Shinyaku Co., Ltd. | Duchenne Muscular Dystrophy | 10/23 | 10/23 | | |
| Active, not recruiting | 3 | 74 | Europe, Canada, Japan, RoW | Viltolarsen, NS-065/NCNP-01 | NS Pharma, Inc., Nippon Shinyaku Co., Ltd. | Duchenne Muscular Dystrophy | 10/25 | 11/25 | | |