Soliris (eculizumab) / AstraZeneca |
NCT01412047: Paroxysmal Nocturnal Hemoglobinuria Human Anti-Human Antibodies Study |
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| Completed | N/A | 75 | US, Europe, RoW | | Alexion Pharmaceuticals | Paroxysmal Nocturnal Hemoglobinuria, PNH | 06/13 | 06/13 | | |
| Approved for marketing | N/A | | US | eculizumab | Alexion Pharmaceuticals | Hemoglobinuria, Paroxysmal | | | | |
| Completed | N/A | 27 | Europe | Blood collection for measurement of eculizumab peak concentrations, blood collection | Radboud University Medical Center | Paroxysmal Nocturnal Hemoglobinuria, Eculizumab, PK-PD | 07/22 | 07/22 | | |
NAP, NCT04671810: Prospective Observational Study of Long-term Pathogenic Treatment of Elizaria® |
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| Completed | N/A | 44 | RoW | Elizaria®, Eculizumab | AO GENERIUM | Paroxysmal Nocturnal Hemoglobinuria | 12/22 | 05/23 | | |
| Available | N/A | | NA | Danicopan, ALXN2040 | Alexion Pharmaceuticals, Inc. | Paroxysmal Nocturnal Hemoglobinuria, PNH, Extravascular Hemolysis | | | | |
ChiCTR2300067949: The real world study of Eculizumab for paroxysmal nocturnal hemoglobinuria treatment in China |
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| Not yet recruiting | N/A | 10 | | Eculizumab | West China Hospitai, Sichuan University; West China Hospitai, Sichuan University, Apply for hospital project funds | paroxysmal nocturnal hemoglobinuria | | | | |