Sarcoma  >>  Ogsiveo (nirogacestat) 
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7 Trials

   

Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
Ogsiveo (nirogacestat) / SpringWorks Therap
DeFi, NCT03785964 / 2018-001991-39: Nirogacestat for Adults With Desmoid Tumor/Aggressive Fibromatosis (DT/AF)

Checkmark Data from DeFi trial for Desmoid Tumors
May 2022 - May 2022: Data from DeFi trial for Desmoid Tumors
Active, not recruiting
3
142
Europe, Canada, US
Nirogacestat oral tablet, PF-03084014, Placebo Oral Tablet
SpringWorks Therapeutics, Inc.
Desmoid Tumor, Aggressive Fibromatosis
04/22
12/24
NCT01981551: Phase II Trial of the Gamma-Secretase Inhibitor PF-03084014 in Adults With Desmoid Tumors/Aggressive Fibromatosis

Completed
2
17
US
PF-03084014
National Cancer Institute (NCI)
Desmoid Tumors, Aggressive Fibromatosis
12/18
12/23
NCT04195399: A Study of a New Drug, Nirogacestat, for Treating Desmoid Tumors That Cannot be Removed by Surgery

Active, not recruiting
2
35
Canada, US, RoW
Biospecimen Collection, Biological Sample Collection, Biospecimen Collected, Specimen Collection, Computed Tomography, CAT, CAT Scan, Computed Axial Tomography, Computerized Axial Tomography, Computerized axial tomography (procedure), Computerized Tomography, Computerized Tomography (CT) scan, CT, CT Scan, tomography, Echocardiography, EC, Magnetic Resonance Imaging, Magnetic Resonance, Magnetic Resonance Imaging (MRI), Magnetic resonance imaging (procedure), Magnetic Resonance Imaging Scan, Medical Imaging, Magnetic Resonance / Nuclear Magnetic Resonance, MR, MR Imaging, MRI, MRI Scan, MRIs, NMR Imaging, NMRI, Nuclear Magnetic Resonance Imaging, sMRI, Structural MRI, Nirogacestat, (S)-2-(((S)-6,8-Difluoro-1,2,3,4-tetrahydronaphthalen-2-yl)amino)-N-(1-(2-methyl-1-(neopentylamino)propan-2-yl)-1H-imidazol-4-yl)pentanamide, PF-03084014, Quality-of-Life Assessment, Quality of Life Assessment, Questionnaire Administration, X-Ray Imaging, Conventional X-Ray, Diagnostic Radiology, Medical Imaging, X-Ray, Plain film radiographs, Radiographic Imaging, Radiographic imaging procedure (procedure), Radiography, RG, Static X-Ray, X-Ray
Children's Oncology Group, National Cancer Institute (NCI), SpringWorks Therapeutics, Inc.
Desmoid Fibromatosis, Recurrent Desmoid Fibromatosis, Unresectable Desmoid Fibromatosis
12/24
12/24
NCT05879146: Evaluation of the Response and Non-response of Nirogacestat in Desmoid Tumors- Clinical Study

Not yet recruiting
2
40
US
Nirogacestat
M.D. Anderson Cancer Center, SpringWorks Therapeutics, Inc.
Tumor
01/27
01/28
NCT05949099: Study of Cryoablation and Nirogacestat for Desmoid Tumor

Recruiting
2
23
US
Nirogacestat, Cryoablation
Stanford University, SpringWorks Therapeutics, Inc.
Desmoid Tumor
02/28
02/28
NCT02955446: Compassionate Use Protocol for PF-03084014 in Patients With Advanced Solid Tumor Malignancies

No Longer Available
N/A
US
PF-03084014, Gamma Secretase Inhibitor
University of Colorado, Denver, SpringWorks Therapeutics, Inc.
Neoplasm, Desmoid Tumor
 
 
NCT05041036: Individual Patient Compassionate Use of Nirogacestat

Available
N/A
NA
Nirogacestat (Gamma Secretase Inhibitor)
SpringWorks Therapeutics, Inc.
Desmoid Tumor, NOTCH Gene Mutation Positive Tumors
 
 

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