NCT00992459: Efficacy and Safety of HPN-100 for the Treatment of Adults With Urea Cycle Disorders |
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| Completed | 3 | 46 | US, Canada | HPN-100, GT4P, glyceryl tri-(4-phenylbutyrate), Buphenyl (NaPBA), sodium phenylbutyrate | Horizon Pharma Ireland, Ltd., Dublin Ireland | Urea Cycle Disorders | 09/10 | 09/10 | | |
NCT01529060: Phenylbutyrate Therapy for Maple Syrup Urine Disease |
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| Completed | 2/3 | 20 | US | Phenylbutyrate, Buphenyl-TM, Placebo powder | Brendan Lee | Maple Syrup Urine Disease | 09/17 | 12/17 | | |