Deficiency Diseases 
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1 Trials

   

Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
Deficiency Diseases
NCT02670889: Urease Inhibitor Drug Treatment for Urea Cycle Disorders

Not yet recruiting
1/2
16
US
Acetohydroxamic Acid, Lithostat, AHA, Isotopic Intravenous [13C]-Urea
Nicholas Ah Mew, Data Management and Coordinating Center (DMCC), Children's Hospital of Philadelphia
Ornithine Transcarbamylase Deficiency, Argininosuccinate Synthetase Deficiency (Citrullinemia), Argininosuccinic Acid Lyase Deficiency (Argininosuccinic Aciduria), Carbamyl-Phosphate Synthase I Deficiency
03/18
03/19

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