Congenital Abnormalities |
| Recruiting | 3 | 250 | Europe | Sirolimus, Rapamycine | Cliniques universitaires Saint-Luc- Université Catholique de Louvain | Vascular Malformations | 04/25 | 04/30 | | |
NCT02258243: Photodynamic Therapy Using Blue Light or Red Light in Treating Basal Cell Carcinoma in Patients With Basal Cell Nevus Syndrome |
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| Active, not recruiting | 2 | 3 | US | aminolevulinic acid hydrochloride, 5-ALA HCl, ALA HCl, aminolevulinic acid HCl, photodynamic therapy, Light Infusion Therapy™, PDT, therapy, photodynamic, laboratory biomarker analysis, questionnaire administration | Case Comprehensive Cancer Center, National Cancer Institute (NCI) | Basal Cell Carcinoma of the Skin, Nevoid Basal Cell Carcinoma Syndrome | 10/16 | 12/17 | | |
| Recruiting | 2 | 500 | Europe | Proton radiotherapy | Uppsala University, Sahlgrenska University Hospital, Sweden, Karolinska University Hospital, University Hospital, Umeå, Region Örebro County, University Hospital, Linkoeping | Central Nervous System Tumour, Arteriovenous Malformation | 07/20 | 07/30 | | |
NCT02137668: Treating Primary Sclerosing Cholangitis and Biliary Atresia With Vancomycin |
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| Recruiting | 1 | 200 | US | Oral Vancomycin, ANI | Sacramento Pediatric Gastroenterology | Primary Sclerosing Cholangitis, Biliary Atresia | 05/18 | 07/28 | | |
| Active, not recruiting | N/A | 650 | US | | National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) | Barrett's Esophagus, Esophageal Neoplasm | | | | |
NCT01322750: Circulating Tumor Cells (CTCs): A Potential Screening Test for Clinically Undetectable Breast Carcinoma |
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| Recruiting | N/A | 3125 | US | | Walter Reed Army Medical Center, Bureau of Navy Medicine (BUMED) | Breast Abnormality | 01/13 | 01/23 | | |
NCT01995305: Use Massive Parallel Sequencing and Exome Capture Technology to Sequence the Exome of Fanconi Anemia Children and Their Patents |
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| Available | N/A | | RoW | human whole exome, whole genomic, whole exome | Xiaofan Zhu | Fanconi Anemia, Autosomal or Sex Linked Recessive Genetic Disease, Bone Marrow Hematopoiesis Failure, Multiple Congenital Abnormalities, and Susceptibility to Neoplastic Diseases., Hematopoiesis Maintainance. | | | | |
NCT00423826: Umbilical Cord Blood Stem Cell Transplant in Treating Patients With Hematologic Cancer or Other Disease |
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| No Longer Available | N/A | | US | Busulfan, Busulfex®, Myleran®, Cytarabine, DepoCyt(TM), Liposomal Ara-C, Fludarabine phosphate, Fludara, mycophenolate mofetil, Cellcept, tacrolimus, Advagraf, Prograf, Protopic, allogeneic hematopoietic stem cell transplantation, umbilical cord blood transplantation, total-body irradiation | Barbara Ann Karmanos Cancer Institute, National Cancer Institute (NCI) | Leukemia, Lymphoma, Multiple Myeloma and Plasma Cell Neoplasm, Myelodysplastic Syndromes, Precancerous Condition, Secondary Myelofibrosis | 01/15 | 01/15 | | |
| No Longer Available | N/A | | NA | SR PIP Implant System | The Hawkins Foundation | Arthrosis, Osteoarthrosis | | | | |
NCT02703831: Single Versus Dual Spine Attending Surgeons in Complex Adult Deformity Surgery: |
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| Not yet recruiting | N/A | 60 | US | Dual attending, Single Attending | Norton Leatherman Spine Center | Scoliosis, Unspecified | 05/18 | 05/23 | | |
| No Longer Available | N/A | | NA | Device closure with the AMPLATZER PFO Occluder | Abbott Medical Devices | Patent Foramen Ovale, Stroke | | | | |
NCT00768703: Percutaneous Endoscopic Tracheal Plug/Unplug for CDH (Congenital Diaphragmatic Hernia) |
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| No Longer Available | N/A | | US | Percutaneous endoscopic fetal tracheal occlusion/unocclusion, Goldvalve Balloon and MiniTorquer Delivery Microcatheter | University of California, San Francisco | Severe Congenital Diaphragmatic Hernia | | | | |
HAEC, NCT02193685: Identification Genetic, Immunologic and Microbial Markers of Hirschsprung Associated Enterocolitis in Children With Hirschsprung Disease |
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| Recruiting | N/A | 400 | US | | Cedars-Sinai Medical Center, Karolinska University Hospital, Children's Hospital Los Angeles, UCSF Benioff Children's Hospital Oakland, University of Michigan, The University of Texas Health Science Center, Houston | Hirschsprung Disease, Enterocolitis | 12/22 | 12/25 | | |
NCT02163603: A Trial on the Opportunity and Treatment of Residual Deformity After Reduction in Developmental Dislocation of the Hip |
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| Not yet recruiting | N/A | 2 | US | Pelvic osteotomy | Hongwen Xu, Tongji Hospital, Wuhan Union Hospital, China, Hunan Children's Hospital, Shenzhen Children's Hospital, Foshan Hospital of Traditional Chinese Medicine, Wuhan Women and Children's Medical Center | Developmental Dislocation of the Hip, Congenital Dislocation of Hip, Residual Deformity, Reduction | 12/24 | | | |
| Active, not recruiting | N/A | 10 | US, Europe | EDI200, APO200 | Edimer Pharmaceuticals | X-linked Hypohidrotic Ectodermal Dysplasia | 03/25 | 03/25 | | |
NCT02014961: Worm Study: Modifier Genes in Sudden Cardiac Death |
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| Recruiting | N/A | 223 | Europe | Dermal biopsy, Gastro-intestinal questionnaire, Whole-exome sequencing | Maastricht University Medical Center, Netherlands Heart Foundation | Brugada Syndrome, Long QT Syndrome 3 | 04/25 | 04/25 | | |
NCT00574327: Progression of Gastroesophageal Reflux Disease and Barrett's Esophagus and the Creation of a Barrett's Registry |
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| Recruiting | N/A | 3000 | US | | Midwest Biomedical Research Foundation, Kansas City Veteran Affairs Medical Center | Barrett's Esophagus, Gastroesophageal Reflux Disease, Esophageal Adenocarcinoma | 10/28 | 01/29 | | |
NCT02581605: Correction of Angular Deformities in Knee Arthrosis |
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| Active, not recruiting | N/A | 84 | Europe | Custom-made 'cutting block' | Imperial College London | Arthritis of Knee | 12/28 | 12/28 | | |
NCT02704455: Registry Study on Primary Ciliary Dyskinesia in Chinese Children |
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| Not yet recruiting | N/A | 100 | RoW | | Beijing Children's Hospital, Shengjing Hospital, Capital Institute of Pediatrics, China, Shanghai Children's Medical Center, Shenzhen Children's Hospital, The First Affiliated Hospital of Xiamen University, First Affiliated Hospital of Guangxi Medical University | Primary Ciliary Dyskinesia | 05/30 | 07/30 | | |
| Recruiting | N/A | 2000 | US | | Pachyonychia Congenita Project | Pachyonychia Congenita | 12/30 | 12/30 | | |
NCT02967822: Molecular Genetic Study of Mayer-Rokitansky-Kuster-Hauser Syndrome |
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| Recruiting | N/A | 410 | Europe | Biological samples for patients, Biological samples for healthy relatives | Imagine Institute, Reference center for rare diseases (Rare Gynecologic Diseases) | Mayer Rokitansky Kuster Hauser Syndrome | 05/31 | 05/31 | | |