NCT02670889: Urease Inhibitor Drug Treatment for Urea Cycle Disorders |
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| Not yet recruiting | 1/2 | 16 | US | Acetohydroxamic Acid, Lithostat, AHA, Isotopic Intravenous [13C]-Urea | Nicholas Ah Mew, Data Management and Coordinating Center (DMCC), Children's Hospital of Philadelphia | Ornithine Transcarbamylase Deficiency, Argininosuccinate Synthetase Deficiency (Citrullinemia), Argininosuccinic Acid Lyase Deficiency (Argininosuccinic Aciduria), Carbamyl-Phosphate Synthase I Deficiency | 03/18 | 03/19 | | |
NCT02233257: Expanded Access for Lorenzo's Oil (GTO/GTE) in Adrenoleukodystrophy |
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| No Longer Available | N/A | | US | Lorenzo's Oil, Glyceryl trierucate | University of Minnesota | X-linked Adrenoleukodystrophy | | | | |