NCT00668564: Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism |
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| Terminated | 2 | 18 | US | Stem Cell Transplantation, Bone Marrow Transplant, cord blood transplant, Cyclophosphamide, Cytoxan, Campath-1H, Alemtuzamab, Busulfan, Busulfex | Masonic Cancer Center, University of Minnesota | Hurler's Syndrome, Maroteaux-Lamy Syndrome, Sly Syndrome, Alpha Mannosidosis, Fucosidosis, Aspartylglucosaminuria, Sphingolipidoses, Krabbe Disease, Wolman's Disease, Niemann-Pick Disease Type B, Niemann-Pick Disease, Type C | 02/10 | 02/10 | | |
