2007-001453-26: Natural course, effects of enzyme therapy and health economic aspects in patients with mucopolysaccharidosis type I, II and VI. Long-term folloe-up of untreated patients and patients receiving commercially available Aldurazyme, Elaprase and Naglazyme. |
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| Ongoing | 4 | 50 | Europe | idursulfase, Naglazyme, Aldurazyme, Elaprase, Naglazyme, Aldurazyme, Elaprase, Naglazyme, Aldurazyme | | Mucopolysaccharidosis type I, II and VI. | | | | |
| Recruiting | 1 | 10 | US | Aldurazyme (laronidase), Elaprase (idursulfase), Vimizim (elosulfase alfa), Naglazyme (galsulfase), Mepsevii (vestronidase alfa-vjbk), Lumizyme (alglucosidase alfa), Kanuma (sebelipase alfa) | University of California, San Francisco, Duke University | MPS I, MPS II, MPS IVA, MPS VI, Mps VII, Gaucher Disease, Type 2, Gaucher Disease, Type 3, Pompe Disease Infantile-Onset, Wolman Disease | 07/31 | 07/32 | | |