Gene transference  >>  Phase 1
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 Phase 
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 Trials
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ezaladcigene resoparvovec (VY-AADC) / Voyager           
          
            
             
AAV-hTERT / Libella Gene Therap           
          
            
             
VGR-R01 / Beijing Tongren Hospital           
          
            
             
FT-003 / Frontera           
          
            
             
GEN2 / GenVivo           
          
            
             
Retinostat (OXB-201) / Oxford Biomedica           
          
            
             
131-I Apamistamab/CAR T-cell (Iomab-ACT) / Actinium           
          
            
             
4D-110 / 4D Molecular Therap, Roche           
          
            
             
AAV1-gSG / Genethon           
          
            
             
AAVrh.10CUhCLN2 / Cornell University, National Institutes of Health           
          
            
             
AXO-AAV-GM2 / Roivant           
          
            
             
Biostrophin (rAAV2.5-CMV-minidystrophin) / Bayer           
          
            
             
CRISPR/Cas9 modified human hematopoietic stem cell therapy / Allife Medical Science and Technology           
          
            
             
CSL200 / CSL Behring           
          
            
             
GZ402663 / Sanofi, AGTC           
          
            
             
HMI-103 / Homology Medicines           
          
            
             
INXN-4001 / Precigen           
          
            
             
KB301 / Krystal Biotech           
          
            
             
KB408 / Krystal Biotech           
          
            
             
LPX EWS/FL1 T1 / Gradalis           
          
            
             
MazF gene therapy / Takara           
          
            
             
RP-L401 / Rocket Pharma           
          
            
             
TN-201 / Tenaya Therap           
          
            
             
TN-401 / Tenaya Therap           
          
            
             
TSHA-120 / Taysha Gene Therapies           
          
            
             
Thalagen (autologous CD34+ cells transduced with TNS9.3.55) / San Rocco Therap, Memorial Sloan-Kettering Cancer Center           
          
            
             
VY-HTT01 / Voyager, Sanofi           
          
            
             
XT-150 intrathecal / Xalud Therap           
          
            
             
humantakinogene hadenovec (PCRX-201) / Pacira