The John Walton Muscular Dystrophy Research Centre - Freeman Hospital - Newcastle University - Institute of Genetic Medicine
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 6 Trials 
3 Trials

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Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
Straub, Volker
Fortify, NCT05775848: Study to Evaluate the Efficacy and Safety of BBP-418 (Ribitol) in Patients With Limb Girdle Muscular Dystrophy 2I (LGMD2I)

Active, not recruiting
3
81
Europe, US, RoW
BBP-418 (ribitol), Placebo
ML Bio Solutions, Inc.
Limb-Girdle Muscular Dystrophy Type 2I (LGMD2I)
07/27
07/27
NCT05224505 / 2021-004276-33: GNT0006 Gene Therapy Trial in Patients With LGMDR9

Recruiting
1/2
39
Europe
GNT0006, Day 0: Placebo, Day 0: GNT0006, Day 365 (year 1): Placebo, Day 365 (year 1): GNT0006
Atamyo Therapeutics, Atamyo Therapeutics
LGMDR9
10/25
10/30
DT4RD, NCT05798325: Feasibility, Validation and Application of Digital Tools for the Follow-up of Neuromuscular Patient Mobility in Daily Living

Recruiting
N/A
40
Europe
2MWT, Two minutes walk tests, MFM32, Muscle Motor Function 32, MyoGrip, QOL-gNMD, Spirometry, Spirobank Smart, Acceleromerty, Links sensor system, 10mWT, PUL, Performance of Upper Limb, NSAA, North Star Ambulatory Assessment, NSAD, North Star Assessment for limb-girdle type muscular dystrophies, TANS, Transition Assessment North Star, MyoPinch, MyoQuad, ACTIVLIM, PREM, Patient Reported Experience Measures, SF-MPQ, Modified Short-form McGill Pain Questionnaire, FSS, Fatigue Severity Scale, IPAQ, International Physical Activity Questionnaire, Rang of motion, EasyAngle, Goniometry, Links Sensor System goniometers, Video captured monitoring, Activity monitoring, Activity assessment and physiological parameters
Institut de Myologie, France, Aparito Ltd.
Neuromuscular Diseases
06/24
06/24
Guglieri, Michaela
No trials found

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