The John Walton Muscular Dystrophy Research Centre - Freeman Hospital - Newcastle University - Institute of Genetic Medicine
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 6 Trials 
9 Trials

   

 
Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
Straub, Volker
Fortify, NCT05775848: Study to Evaluate the Efficacy and Safety of BBP-418 (Ribitol) in Patients With Limb Girdle Muscular Dystrophy 2I (LGMD2I)

Active, not recruiting
3
81
Europe, US, RoW
BBP-418 (ribitol), Placebo
ML Bio Solutions, Inc.
Limb-Girdle Muscular Dystrophy Type 2I (LGMD2I)
07/27
07/27
NCT05224505 / 2021-004276-33: GNT0006 Gene Therapy Trial in Patients With LGMDR9

Recruiting
1/2
39
Europe
GNT0006, Day 0: Placebo, Day 0: GNT0006, Day 365 (year 1): Placebo, Day 365 (year 1): GNT0006
Atamyo Therapeutics, Atamyo Therapeutics
LGMDR9
10/25
10/30
NCT04001595: Global FKRP Registry

Recruiting
N/A
1000
Europe
Patient Registry
Newcastle University, LGMD2i Research Fund, CureLGMD2i, Ludwig-Maximilians - University of Munich
LGMD2I, LGMDR9, Limb Girdle Muscular Dystrophy, Congenital Muscular Dystrophy, Muscle-Eye-Brain Disease, Walker-Warburg Syndrome, FKRP Gene Mutation
12/25
12/25
NCT04583917: Brain Involvement in Dystrophinopathies Part 1

Completed
N/A
377
Europe
Great Ormond Street Hospital for Children NHS Foundation Trust, Newcastle-upon-Tyne Hospitals NHS Trust, Leiden University Medical Center, Stichting Kempenhaeghe, Region Hovedstadens Apotek, Institut Necker Enfants Malades, Catholic University of the Sacred Heart, Università degli Studi di Ferrara, Universidad Complutense de Madrid
Duchenne Muscular Dystrophy, Becker Muscular Dystrophy
06/24
06/24
Jain COS, NCT01676077: Clinical Outcome Study for Dysferlinopathy

Active, not recruiting
N/A
200
Europe, Japan, US, RoW
Newcastle-upon-Tyne Hospitals NHS Trust, Jain Foundation
Dysferlinopathy, LGMD2B Now Classified as LGMDR2, Miyoshi Myopathy
03/24
03/24
NCT04668716: Brain Involvement in Dystrophinopathies Part 2

Completed
N/A
339
Europe
Great Ormond Street Hospital for Children NHS Foundation Trust, Newcastle-upon-Tyne Hospitals NHS Trust, Leiden University Medical Center, Stichting Kempenhaeghe, Region Hovedstadens Apotek, Institut Necker Enfants Malades, Catholic University of the Sacred Heart, Università degli Studi di Ferrara, Universidad Complutense de Madrid
Duchenne Muscular Dystrophy, Becker Muscular Dystrophy
06/24
06/24
DT4RD, NCT05798325: Feasibility, Validation and Application of Digital Tools for the Follow-up of Neuromuscular Patient Mobility in Daily Living

Recruiting
N/A
40
Europe
2MWT, Two minutes walk tests, MFM32, Muscle Motor Function 32, MyoGrip, QOL-gNMD, Spirometry, Spirobank Smart, Acceleromerty, Links sensor system, 10mWT, PUL, Performance of Upper Limb, NSAA, North Star Ambulatory Assessment, NSAD, North Star Assessment for limb-girdle type muscular dystrophies, TANS, Transition Assessment North Star, MyoPinch, MyoQuad, ACTIVLIM, PREM, Patient Reported Experience Measures, SF-MPQ, Modified Short-form McGill Pain Questionnaire, FSS, Fatigue Severity Scale, IPAQ, International Physical Activity Questionnaire, Rang of motion, EasyAngle, Goniometry, Links Sensor System goniometers, Video captured monitoring, Activity monitoring, Activity assessment and physiological parameters
Institut de Myologie, France, Aparito Ltd.
Neuromuscular Diseases
06/24
06/24
NCT04020159: Global Registry for COL6-related Dystrophies

Recruiting
N/A
1000
Europe
Patient Registry
Newcastle-upon-Tyne Hospitals NHS Trust
Bethlem Myopathy, Ullrich Congenital Muscular Dystrophy 1, Digenic, Col6A1/Col6A2, Ullrich Congenital Muscular Dystrophy 1, Autosomal Recessive, Ullrich Congenital Muscular Dystrophy 1, Autosomal Dominant, Bethlem Myopathy 1, Autosomal Recessive, UCMD, BTHLM1
10/24
10/24
NCT06324188: Early Atrial Fibrillation Ablation for Stroke Prevention in Patients with High Comorbidity Burden (EASThigh-AFNET 11)

Recruiting
N/A
2312
Europe, Canada, RoW
Early atrial fibrillation ablation, Usual Care
Atrial Fibrillation Network
Atrial Fibrillation
02/30
05/30
Guglieri, Michaela
No trials found

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