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Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
Aleman, Tomas
NCT05616793: Safety and Tolerability Subretinal OPGx-001 for LCA5-Associated Inherited Retinal Degeneration (LCA5-IRD)	Recruiting	1/2	15	US	AAV8.hLCA5	Opus Genetics, Inc, University of Pennsylvania	LCA5	12/24	01/28
LIGHTHOUSE, NCT05878860: ATSN-201 Gene Therapy in RS1-Associated X-linked Retinoschisis	Recruiting	1/2	21	US	ATSN-201	Atsena Therapeutics Inc.	X-linked Retinoschisis	10/25	10/29
Pearson, Denise
NCT03969992: A Dose-Ranging Study to Determine the Efficacy, Safety and Tolerability of AeroFact	Completed	2	261	Canada, US	AeroFact, SF-RI 1, nCPAP	Aerogen Pharma Limited	Respiratory Distress Syndrome in Premature Infant	08/23	08/24