University Hospitals of Cleveland/Rainbow Babies and Children's Hospital
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 3 Trials 
5 Trials

   

Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
McCandless, Shawn
VNS4PWS, NCT06144645: A Clinical Evaluation of Non-Invasive Vagus Nerve Stimulation for Temper Outbursts in People with PWS

Recruiting
3
102
US
tVNS, intermittent stimulation, tVNS R, manufactured by tVNS Technologies, intermittent stimulation, tVNS, continuous stimulation, tVNS R, manufactured by tVNS Technologies, continuous stimulation
Foundation for Prader-Willi Research, RTI International
Prader-Willi Syndrome
12/26
12/27
NCT06366464: A Study of Pitolisant in Patients with Prader-Willi Syndrome

Recruiting
3
134
US
Pitolisant tablet, pitolisant, Placebo tablet, placebo
Harmony Biosciences, LLC
Prader-Willi Syndrome
07/26
07/27
NCT05153434: A Study of Oral ARD-101 in Patients With Prader-Willi Syndrome

Active, not recruiting
2
18
US
ARD-101
Aardvark Therapeutics, Inc., Children's Hospital Colorado, Stanford University
Prader-Willi Syndrome
11/24
02/25
NCT04612764: Liver Disease in Urea Cycle Disorders

Recruiting
N/A
62
US
Baylor College of Medicine, Children's National Research Institute, Seattle Children's Hospital, Children's Hospital Colorado, Children's Hospital of Philadelphia
Urea Cycle Disorder, Ornithine Transcarbamylase Deficiency, Citrullinemia 1, ARGI Deficiency, ASL Deficiency, Argininosuccinic Aciduria, ASS Deficiency, Hyperargininemia
12/24
12/24
NCT00237315: Longitudinal Study of Urea Cycle Disorders

Recruiting
N/A
1500
Europe, Canada, US
Andrea Gropman, National Center for Research Resources (NCRR), Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD), Rare Diseases Clinical Research Network
Brain Diseases, Metabolic, Inborn, Amino Acid Metabolism, Inborn Errors, Urea Cycle Disorders
07/25
07/26
Heggie, Christine
No trials found

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