| Attarian, Shahram |
| Terminated | 3 | 489 | Europe, Canada, US, RoW | Reldesemtiv, Placebo | Cytokinetics | Amyotrophic Lateral Sclerosis | 07/23 | 07/23 | | |
| Active, not recruiting | 3 | 187 | Europe, Canada, US | PXT3003 | Pharnext S.C.A., Synteract HCR (Syneos Health), Premier Research Group plc, Greenphire, Theradis, Amarex, Eurofins Optimed | Charcot-Marie-Tooth Disease, Type IA | 12/24 | 12/24 | | |
THERAMAG, NCT05136976: Rituximab Therapy in Anti-Myelin Associated Glycoprotein Patients With Characteristics of Good Responders |
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| Recruiting | 3 | 90 | Europe | Rituximab infusion, Mabthera, Placebo infusion, Sodium chloride (NaCl), Premedications | Centre Hospitalier Universitaire de Saint Etienne, Ministry of Health, France | Anti-MAG Neuropathy | 12/25 | 12/25 | | |
| Completed | 2 | 30 | Europe | Imlifidase, Hansa Medical-Immunoglobulin G degrading enzyme of Streptococcus pyogenes (HMED-IdeS), IdeS, IgG endopeptidase | Hansa Biopharma AB, Hansa Biopharma AB | Guillain-Barré Syndrome (GBS) | 02/24 | 02/24 | | |
| Active, not recruiting | 2 | 51 | Europe | IFB-088 50mg/day, IFB-088, Icerguastat, Placebo, Riluzole 100mg/day, Riluzole | InFlectis BioScience, InFlectis BioScience, | Amyotrophic Lateral Sclerosis, ALS | 01/25 | 01/25 | | |
NCT06436742: A Phase 1b Study to Investigate Safety and Tolerability of ARGX-119 in Adult Participants with DOK7-Congenital Myasthenic Syndromes (CMS) |
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| Recruiting | 1 | 15 | Europe, Canada, US | ARGX-119, Placebo | argenx | Congenital Myasthenic Syndrome | 10/25 | 10/25 | | |
| Completed | N/A | 251 | Europe | Neurological assessment and Blood sample | Centre Hospitalier Universitaire de Saint Etienne | Sensory Peripheral Neuropathy | 11/21 | 01/22 | | |
FG-CoALS, NCT06147843: French-German Cohort Study to Determine Factors Associated With Weight Loss in Amyotrophic Lateral Sclerosis |
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| Recruiting | N/A | 1000 | Europe | Blood sample | University Hospital, Limoges, National Research Agency, France, Centre de Recherche en biomédecine de Strasbourg INSERM UMR-S1118, Institut du Cerveau et de la Moelle épinière, Institut National de la Santé et de la Recherche Médical - délégation Grand Ouest INSERM U1253, Klinik für Neurologie, Universitäts- und Rehabilitationskliniken Ulm (RKU), Centre de Données Cliniques et de Recherche CDCR, UMR Inserm U1253-IBRain-Neurogénétique et Physiopathologie Neuronale, France Cohorte | Amyotrophic Lateral Sclerosis | 09/27 | 09/29 | | |
NCT06078553: A Natural History Study in Participants With DOK7 Congenital Myasthenic Syndromes (CMS) |
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| Recruiting | N/A | 30 | Europe, Canada, US | | argenx | Congenital Myasthenic Syndrome | 07/25 | 07/25 | | |
SMAII, NCT04159987: Monitoring to the Evolution of Motor Function in SMA Type II Adults Patients Treated With SPINRAZA® |
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| Completed | N/A | 20 | Europe | Spinraza intrathecal injection | Centre Hospitalier Universitaire de Nice | Spinal Muscular Atrophy | 07/24 | 07/24 | | |
| Active, not recruiting | N/A | 413 | Europe, Canada, Japan, US, RoW | | argenx | Multifocal Motor Neuropathy | 11/25 | 11/25 | | |
INSIGHT FSHD2, NCT06079567: An 18-month Prospective Natural History Study to Gain Insight Into FSHD2 Pathophysiology and Disease Progression |
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| Recruiting | N/A | 50 | Europe | Validation of new COMs for FSHD2 patients | Centre Hospitalier Universitaire de Nice | Facioscapulohumeral Muscular Dystrophy Type 2 | 04/26 | 04/26 | | |
CMT-TOOLS, NCT02596191: Tools for Therapeutic Evaluation in Charcot-Marie-Tooth Disease Type 1A: Outcome Measures and Biomarkers |
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| Recruiting | N/A | 80 | Europe | Clinical evaluation, electrophysiological record, Muscle MRI, blood samples analysis | Assistance Publique Hopitaux De Marseille | Charcot-Marie-Tooth Disease Type 1A | 06/26 | 12/27 | | |
| Recruiting | N/A | 66 | Europe | diagnosis of mitochondrial myopathy | Centre Hospitalier Universitaire de Nice | Mitochondrial Diseases | 03/22 | 09/25 | | |
| Denis, Danièle |
NCT04725760: Evaluation of the Efficacy of the BrainPort Vision Pro on the Performance of Daily Activities in the Profoundly Blind French Population |
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| Recruiting | N/A | 125 | Europe | BrainPort Vision Pro | Wicab | Blindness | 09/22 | 09/22 | | |
