| Recruiting | 3 | 5000 | Europe, RoW | Blinatumomab, Bortezomib, Cyclophosphamide, Cytarabine, Daunorubicin, Myocet, Dexamethasone, Doxorubicin, Etoposide, Fludarabine Phosphate, Ifosfamide, 6-Mercaptopurine, Methotrexate, Pegaspargase, Prednisolone, Prednisone, Tioguanin, Vincristine, Vindesine, Erwinase | Martin Schrappe, Deutsche Krebshilfe e.V., Bonn (Germany) | Acute Lymphoblastic Leukemia, Pediatric | 07/28 | 07/28 | | |
| Recruiting | 2 | 45 | Europe | Sirolimus 0.5 mg | Università degli Studi di Ferrara, Rare Partners srl Impresa Sociale, Azienda Ospedaliero, Universitaria Meyer, Azienda Ospedaliero, Universitaria Pisana | Beta-Thalassemia | 04/22 | 04/22 | | |
| Recruiting | 2 | 89 | Europe, RoW | Mylotarg, GO, Arsenic Trioxide, ATO, All-trans retinoic acid, ATRA | Associazione Italiana Ematologia Oncologia Pediatrica, AIEOP | Acute Promyelocytic Leukemia | 10/25 | 10/27 | | |