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Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
Gillis, Lynette
NCT03115086: The REPLACE Registry for Cholbam® (Cholic Acid)	Active, not recruiting	N/A	55	US	Cholbam	Mirum Pharmaceuticals, Inc.	Bile Acid Synthesis Disorders	07/38	07/39
Owens, Eugenia
CSIDE, NCT03619551: Conditioning SCID Infants Diagnosed Early	Recruiting	2	64	Canada, US	Busulfan, Cell processing for TCRαβ+/CD19+ depletion, CliniMACS	Michael Pulsipher, MD	SCID	08/26	08/26
CASSIOPEIA, NCT03876769 / 2017-002116-14: Study of Efficacy and Safety of Tisagenlecleucel in HR B-ALL EOC MRD Positive Patients Jan 2025 - Dec 2025: Data from CASSIOPEIA trial for 1L acute ALL	Recruiting	2	121	Europe, Canada, US	CTL019	Novartis Pharmaceuticals, Children's Oncology Group	B-Cell Acute Lymphoblastic Leukemia	10/27	10/27
NCT01590680: Expanded Access Protocol Using 131I-MIBG	Available	N/A		US	I-131 MIBG, I-131 Iobenguane, I-131 meta-iodobenzylguanidine	Jubilant DraxImage Inc.	Neuroblastoma, Pheochromocytoma, Paraganglioma
Heuer, Mykala
No trials found