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Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
Gan, Richard
ATLAS, NCT04856982 / 2020-004590-51: A Study of BIIB067 (Tofersen) Initiated in Clinically Presymptomatic Adults With a Confirmed Superoxide Dismutase 1 Mutation	Recruiting	3	150	Europe, Canada, Japan, US, RoW	Tofersen, BIIB067, QALSODY, Placebo	Biogen	Amyotrophic Lateral Sclerosis Associated With a SOD1 Gene Mutation	08/27	08/27
REAL, NCT05218668: Rho Kinase Inhibitor in Amyotrophic Lateral Sclerosis	Active, not recruiting	2	40	US, RoW	Fasudil (WP-0512)	Woolsey Pharmaceuticals	Amyotrophic Lateral Sclerosis	07/26	01/28
NCT05882695: Study of SPG302 in Healthy Volunteers and ALS Participants	Active, not recruiting	1	112	RoW	SPG302, Placebo	Spinogenix, Novotech (Australia) Pty Limited	Amyotrophic Lateral Sclerosis	05/25	12/25
Griffin, Kaitlyn
AS-001, NCT05011851: An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Angelman Syndrome	Completed	2	16	RoW	NNZ-2591, Cyclo-L-Glycyl-L-2-Allylproline	Neuren Pharmaceuticals Limited	Angelman Syndrome	05/24	07/24
Purcell, Carley
MyeChild 01, NCT02724163 / 2014-005066-30: International Randomised Phase III Clinical Trial in Children With Acute Myeloid Leukaemia	Recruiting	3	700	Europe, RoW	Gemtuzumab ozogamicin, Mylotarg, Liposomal daunorubicin, Mitoxantrone, Fludarabine, Cytarabine, Busulfan, Cyclophosphamide	University of Birmingham, Assistance Publique - Hôpitaux de Paris, Cancer Research UK, National Cancer Institute, France, Pfizer	Acute Myeloid Leukaemia	12/31	12/32