BEGIN, NCT04509050: Study to Evaluate Biological & Clinical Effects of Significantly Corrected CFTR Function in Infants & Young Children |
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| Recruiting | N/A | 210 | US | Ivacaftor or elexacaftor/tezacaftor/ivacaftor, Kalydeco or Trikafta, Vertex (VX)-770 or VX-445/VX-661/VX-770 | Sonya Heltshe, Cystic Fibrosis Foundation, University of Washington, University of Alabama at Birmingham | Cystic Fibrosis | 12/29 | 12/29 | | |