PTC Clinical Site 2
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 1 Trial 
2 Trials

   

Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
Hamazaki, Takashi
NCT05166161 / 2021-000497-28: A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria

Recruiting
3
200
Europe, Canada, Japan, US, RoW
PTC923, Sepiapterin
PTC Therapeutics
Phenylketonuria
04/26
04/26
NCT06895746: Multi-omics Study in Citrin Deficiency

Recruiting
N/A
100
Europe, Japan, US, RoW
Johannes Haeberle, Citrin Foundation, Bristol Royal Hospital for Children, Central Manchester University Hospital NHS Foundation Trust, University Hospital Birmingham NHS Foundation Trust, Northern Care Alliance NHS Foundation Trust, Mount Sinai Hospital, New York, National Taiwan University Hospital, Taipei Veterans General Hospital, Taiwan, Pusan National University Yangsan Hospital, Saitama Medical University, Osaka Metropolitan University, Tohoku University, Kurume University, University College London Hospitals, Sheffield Children's NHS Foundation Trust, Great Ormond Street Hospital for Children NHS Foundation Trust, Kumamoto University, Saiseikai Yokohama City Eastern Hospital, Jikei University School of Medicine, Yamagata University, Chiba Children's Hospital, Shinshu University Hospital, Birmingham Women's and Children's NHS Foundation Trust, National Hospital Organisation Hokkaido Medical Center
Citrin Deficiency
12/25
12/25
Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
Hamazaki, Takashi
NCT05166161 / 2021-000497-28: A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria

Recruiting
3
200
Europe, Canada, Japan, US, RoW
PTC923, Sepiapterin
PTC Therapeutics
Phenylketonuria
04/26
04/26
NCT06895746: Multi-omics Study in Citrin Deficiency

Recruiting
N/A
100
Europe, Japan, US, RoW
Johannes Haeberle, Citrin Foundation, Bristol Royal Hospital for Children, Central Manchester University Hospital NHS Foundation Trust, University Hospital Birmingham NHS Foundation Trust, Northern Care Alliance NHS Foundation Trust, Mount Sinai Hospital, New York, National Taiwan University Hospital, Taipei Veterans General Hospital, Taiwan, Pusan National University Yangsan Hospital, Saitama Medical University, Osaka Metropolitan University, Tohoku University, Kurume University, University College London Hospitals, Sheffield Children's NHS Foundation Trust, Great Ormond Street Hospital for Children NHS Foundation Trust, Kumamoto University, Saiseikai Yokohama City Eastern Hospital, Jikei University School of Medicine, Yamagata University, Chiba Children's Hospital, Shinshu University Hospital, Birmingham Women's and Children's NHS Foundation Trust, National Hospital Organisation Hokkaido Medical Center
Citrin Deficiency
12/25
12/25

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