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Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
Baghdasaryan, Anna
NCT06582524: Pegzilarginase in Subjects <24 Months Old with Arginase 1 Deficiency	Recruiting	3	3	Europe	Pegzilarginase, Loargys	Immedica Pharma AB	Arginase 1 Deficiency	12/25	12/25
NCT06729554: Education & Care in RARE: Efficacy of Targeted Psychoeducational Intervention Among Pediatric Rare Disease Patients	Recruiting	N/A	100	Europe	Education & Care in RARE	Medical University of Vienna	Orphan Diseases, Rare Disorders, Pediatric Diseases, Inborn Errors of Metabolism Disorders	12/26	12/26