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Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
Anikster, Yair
NCT06214507: Danon Disease Natural History Study	Recruiting	N/A	46	Europe, US, RoW	No intervention	Rocket Pharmaceuticals Inc.	Danon Disease	08/26	08/26
NCT06474104: Collection of Blood and Skin Samples From Patients With Primary Mitochondrial Diseases and Healthy Volunteers	Recruiting	N/A	100	RoW		Minovia Therapeutics Ltd.	Primary Mitochondrial Diseases	05/25	05/26
Rossano, Joseph
NCT06092034: A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease	Active, not recruiting	2	12	Europe, US	RP-A501	Rocket Pharmaceuticals Inc.	Danon Disease	09/25	09/29
NCT03882437: Gene Therapy for Male Patients With Danon Disease (DD) Using RP-A501; AAV9.LAMP2B	Active, not recruiting	1	7	US	RP-A501	Rocket Pharmaceuticals Inc.	Danon Disease	03/25	03/25
NCT05885412: A Phase 1, Dose Escalation Trial of RP-A601 in Subjects With PKP2 Variant-Mediated Arrhythmogenic Cardiomyopathy (PKP2-ACM)	Recruiting	1	9	US	RP-A601	Rocket Pharmaceuticals Inc.	PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM)	09/25	09/26
NCT06214507: Danon Disease Natural History Study	Recruiting	N/A	46	Europe, US, RoW	No intervention	Rocket Pharmaceuticals Inc.	Danon Disease	08/26	08/26
Garuba, David
NCT06214507: Danon Disease Natural History Study	Recruiting	N/A	46	Europe, US, RoW	No intervention	Rocket Pharmaceuticals Inc.	Danon Disease	08/26	08/26