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Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
Latif, Farhana
NCT06214507: Danon Disease Natural History Study	Recruiting	N/A	46	Europe, US, RoW	No intervention	Rocket Pharmaceuticals Inc.	Danon Disease	08/26	08/26
Wolf, Cordula
NCT06092034: A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease	Active, not recruiting	2	12	Europe, US	RP-A501	Rocket Pharmaceuticals Inc.	Danon Disease	09/25	09/29
NCT06214507: Danon Disease Natural History Study	Recruiting	N/A	46	Europe, US, RoW	No intervention	Rocket Pharmaceuticals Inc.	Danon Disease	08/26	08/26
Hope, Kyle
NCT06214507: Danon Disease Natural History Study	Recruiting	N/A	46	Europe, US, RoW	No intervention	Rocket Pharmaceuticals Inc.	Danon Disease	08/26	08/26

Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
Latif, Farhana
NCT06214507: Danon Disease Natural History Study	Recruiting	N/A	46	Europe, US, RoW	No intervention	Rocket Pharmaceuticals Inc.	Danon Disease	08/26	08/26
Wolf, Cordula
NCT06092034: A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease	Active, not recruiting	2	12	Europe, US	RP-A501	Rocket Pharmaceuticals Inc.	Danon Disease	09/25	09/29
NCT06214507: Danon Disease Natural History Study	Recruiting	N/A	46	Europe, US, RoW	No intervention	Rocket Pharmaceuticals Inc.	Danon Disease	08/26	08/26
Hope, Kyle
NCT06214507: Danon Disease Natural History Study	Recruiting	N/A	46	Europe, US, RoW	No intervention	Rocket Pharmaceuticals Inc.	Danon Disease	08/26	08/26