| Recruiting | N/A | 5000 | Europe | | CENTOGENE GmbH Rostock, Alnylam Pharmaceuticals | Transthyretin Amyloidosis, Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy, Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy, Polyneuropathies, Cardiomyopathies | 04/25 | 04/25 | | |
| Active, not recruiting | N/A | 413 | Europe, Canada, Japan, US, RoW | | argenx | Multifocal Motor Neuropathy | 11/25 | 11/25 | | |