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Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
Debien, Elisa
SYNAPSE-SMA, NCT05794139 / 2022-002301-24: Safety and Efficacy of NMD670 in Ambulatory Adult Patients With Type 3 Spinal Muscular Atrophy	Recruiting	2	54	Europe, Canada, US	NMD670, Placebo	NMD Pharma A/S, NMD Pharma A/S	Spinal Muscular Atrophy	07/25	07/25
Wong, Berchman
ATLAS, NCT04856982 / 2020-004590-51: A Study of BIIB067 (Tofersen) Initiated in Clinically Presymptomatic Adults With a Confirmed Superoxide Dismutase 1 Mutation	Recruiting	3	150	Europe, Canada, Japan, US, RoW	Tofersen, BIIB067, QALSODY, Placebo	Biogen	Amyotrophic Lateral Sclerosis Associated With a SOD1 Gene Mutation	08/27	08/27
SYNAPSE-SMA, NCT05794139 / 2022-002301-24: Safety and Efficacy of NMD670 in Ambulatory Adult Patients With Type 3 Spinal Muscular Atrophy	Recruiting	2	54	Europe, Canada, US	NMD670, Placebo	NMD Pharma A/S, NMD Pharma A/S	Spinal Muscular Atrophy	07/25	07/25