SESAM, NCT05577754: Assessment of the Efficacy and Safety of Alpelisib (BYL719) in Pediatric and Adult Patients With Megalencephaly-CApillary Malformation Polymicrogyria Syndrome (MCAP) |
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| Recruiting | 2 | 20 | Europe | Alpelisib (BYL719), Matching placebo, Optional lumbar puncture + blood sample | Centre Hospitalier Universitaire Dijon, Novartis Pharmaceuticals | Megalencephaly-capillary Malformation Polymicrogyria Syndrome (MCAP) | 03/27 | 03/27 | | |