Washington University in St. Louis/St. Louis Children's Hospital
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 1 Trial 
6 Trials

   

Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
Novak, Olga
NEOS, NCT04926818 / 2020-002700-39: Efficacy and Safety of Ofatumumab and Siponimod Compared to Fingolimod in Pediatric Patients With Multiple Sclerosis

Active, not recruiting
3
129
Europe, Canada, US, RoW
Fingolimod, FTY720, Ofatumumab, OMB157, Siponimod, BAF312, Fingolimod placebo, Siponimod placebo, Ofatumumab placebo
Novartis Pharmaceuticals, Novartis Pharma AG
Multiple Sclerosis (MS)
03/27
11/31
TSC-STEPS, NCT05104983: Stopping TSC Onset and Progression 2B: Sirolimus TSC Epilepsy Prevention Study

Recruiting
2
64
US
Sirolimus, Placebo
Darcy Krueger
Tuberous Sclerosis Complex, Epilepsy
06/25
06/26
ICCRN, NCT05558371: International CDKL5 Clinical Research Network

Recruiting
N/A
1000
US, RoW
No intervention.
University of Colorado, Denver, National Institute of Neurological Disorders and Stroke (NINDS), National Institutes of Health (NIH), International Foundation for CDKL5 Research
CDKL5, CDKL5 Deficiency Disorder, CDD
02/26
02/27
Weisenberg, Judith
ICCRN, NCT05558371: International CDKL5 Clinical Research Network

Recruiting
N/A
1000
US, RoW
No intervention.
University of Colorado, Denver, National Institute of Neurological Disorders and Stroke (NINDS), National Institutes of Health (NIH), International Foundation for CDKL5 Research
CDKL5, CDKL5 Deficiency Disorder, CDD
02/26
02/27
Abila, Maria
CANDID, NCT05373719: Observational Study in Patients With Cyclin-dependent Kinase-like 5 Deficiency Disorder

Active, not recruiting
N/A
112
Europe, Canada, US, RoW
No intervention; observational
Loulou Foundation
Cyclin-Dependent Kinase-Like 5 Deficiency Disorder
01/27
01/27
ICCRN, NCT05558371: International CDKL5 Clinical Research Network

Recruiting
N/A
1000
US, RoW
No intervention.
University of Colorado, Denver, National Institute of Neurological Disorders and Stroke (NINDS), National Institutes of Health (NIH), International Foundation for CDKL5 Research
CDKL5, CDKL5 Deficiency Disorder, CDD
02/26
02/27

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