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Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
Mistry, Pramod
LEAP2MONO, NCT05222906 / 2021-005402-10: Study to Evaluate the Efficacy and Safety of Venglustat in Adult and Pediatric Patients With Gaucher Disease Type 3	Active, not recruiting	3	43	Europe, Canada, Japan, US, RoW	Venglustat, imiglucerase, Cerezyme®	Sanofi, Sanofi-aventis recherche & développement	Gaucher's Disease Type III	09/25	10/26
NCT05239858: International Wilson's Disease Patient Registry (iWilson Registry)	Recruiting	N/A	500	Europe, RoW		Orphalan, Ergomed	Wilson's Disease	12/27	12/27
Yang, Ruhua
LEAP2MONO, NCT05222906 / 2021-005402-10: Study to Evaluate the Efficacy and Safety of Venglustat in Adult and Pediatric Patients With Gaucher Disease Type 3	Active, not recruiting	3	43	Europe, Canada, Japan, US, RoW	Venglustat, imiglucerase, Cerezyme®	Sanofi, Sanofi-aventis recherche & développement	Gaucher's Disease Type III	09/25	10/26